Highlights From the WFH 2022 World Congress
Using the World Federation of Haemophilia Gene Therapy Registry for the Long-term Follow-up of Haemophilia Patients Treated with Gene Therapy
Presented by: Barbara A. Konkle, MD, University of Washington, Seattle, Washington, USA
Barbara A. Konkle1, Donna Coffin2, Mayss Naccache2, Cary Clark3, Lindsey A. George4, Alfonso Iorio5, Wolfgang Miesbach6, Declan Noone7, Flora Peyvandi8, Steven Pipe9, Michael Recht10, Mark Skinner11, Leonard Valentino12, Johnny N. Mahlangu13, Glenn F. Pierce2
1University of Washington, Seattle, United States
2World Federation of Hemophilia, Montreal, Canada
3International Society on Thrombosis and Haemostasis, Carrboro, United States
4The Children’s Hospital of Philadelphia, Philadelphia, United States
5Department of Health Research Methods, Evidence, and Impact, McMaster University, Hamilton, Canada
6Medical Clinic 2/Institute of Transfusione Medicine University Hospital Frankfurt, Germany
7European Haemophilia Consortium, Belgium
8Università degli Studi di Milano, Italy
9Departments of Pediatrics and Pathology, University of Michigan, Ann Arbor, United States
10American Thrombosis and Hemostasis Network, Rochester, United States
11Institutefor Policy Advancement Ltd., and Department of Health Research Methods, Evidence, and Impact, McMaster University, Washington, District of Columbia
12National Hemophilia Foundation, New York, United States
13University of the Witwatersrand, South Africa