Mga Highlight Mula sa ISTH 2021 Congress
Kahusayan at Kaligtasan ng Valoctocogene Roxaparvovec Adeno na nauugnay sa Virus Gene Transfer para sa Malubhang Hemophilia A: Mga Resulta Mula sa Phase 3 GENEr8-1 Trial
MC Ozelo1, J. Mahlangu2, KJ. Pasi3, A. Giermasz4, AD Leavitt5, M. Laffan6, E. Symington7, DV Quon8, J.-D. Wang9, K. Peerlink11, S. Pipe11, B. Madan12, NS Key13, GF Pierce14, B. O'Mahony15,16, R. Kaczmarek17,18, A. Batas19, M. Huang19, WY Wong19, B. Kim19, GENER8-1 Trial Group
1Hemocentro UNICAMP, Kagawaran ng Panloob na Gamot, School of Medical Science, University of Campinas, Campinas, Brazil
2Hemophilia Comprehensive Care Center, Charlotte Maxeke Johannesburg Academic Hospital, University of the Witwatersrand at NHLS, Johannesburg, South Africa
3Barts at London School of Medicine and Dentistry, London, United Kingdom
4Hemophilia Treatment Center, University of California Davis, Sacramento, Estados Unidos
5University of California, San Francisco, Estados Unidos
6Center para sa Hematology, Imperial College London, London, United Kingdom
7Mga Pamantasan sa University of Cambridge NHS Foundation Trust, Cambridge, United Kingdom
8Orthopaedic Hemophilia Treatment Center, Los Angeles, Estados Unidos
9Center for Rare Disease and Hemophilia, Taichung Veterans General Hospital, Taichung, Taiwan, Lalawigan ng Tsina
10Kagawaran ng Vascular Medicine at Haemostasis at Haemophilia Center, University Hospitals Leuven, Leuven, Belgium
11Mga Kagawaran ng Pediatrics and Pathology, University of Michigan, Ann Arbor, Estados Unidos
12NHS Foundation Trust ng Guy at St. Thomas ', London, United Kingdom
13UNC Blood Research Center, University of North Carolina, Chapel Hill, Estados Unidos
14Independent Consultant, La Jolla, Estados Unidos
15Irish Haemophilia Society, Dublin, Ireland
16Trinity College, Dublin, Ireland
17Kagawaran ng Pediatrics, Indiana University School of Medicine, IUPUI-Wells Center para sa Pediatric Research, Indianapolis, Estados Unidos
18Laboratory of Glycobiology, Hirszfeld Institute of Immunology at Experimental Therapy, Wroclaw, Poland
19BioMarin Pharmaceutical Inc., Novato, Estados Unidos
MC Ozelo1, J. Mahlangu2, KJ. Pasi3, A. Giermasz4, AD Leavitt5, M. Laffan6, E. Symington7, DV Quon8, J.-D. Wang9, K. Peerlink11, S. Pipe11, B. Madan12, NS Key13, GF Pierce14, B. O'Mahony15,16, R. Kaczmarek17,18, A. Batas19, M. Huang19, WY Wong19, B. Kim19, GENER8-1 Trial Group
1Hemocentro UNICAMP, Kagawaran ng Panloob na Gamot, School of Medical Science, University of Campinas, Campinas, Brazil
2Hemophilia Comprehensive Care Center, Charlotte Maxeke Johannesburg Academic Hospital, University of the Witwatersrand at NHLS, Johannesburg, South Africa
3Barts at London School of Medicine and Dentistry, London, United Kingdom
4Hemophilia Treatment Center, University of California Davis, Sacramento, Estados Unidos
5University of California, San Francisco, Estados Unidos
6Center para sa Hematology, Imperial College London, London, United Kingdom
7Mga Pamantasan sa University of Cambridge NHS Foundation Trust, Cambridge, United Kingdom
8Orthopaedic Hemophilia Treatment Center, Los Angeles, Estados Unidos
9Center for Rare Disease and Hemophilia, Taichung Veterans General Hospital, Taichung, Taiwan, Lalawigan ng Tsina
10Kagawaran ng Vascular Medicine at Haemostasis at Haemophilia Center, University Hospitals Leuven, Leuven, Belgium
11Mga Kagawaran ng Pediatrics and Pathology, University of Michigan, Ann Arbor, Estados Unidos
12NHS Foundation Trust ng Guy at St. Thomas ', London, United Kingdom
13UNC Blood Research Center, University of North Carolina, Chapel Hill, Estados Unidos
14Independent Consultant, La Jolla, Estados Unidos
15Irish Haemophilia Society, Dublin, Ireland
16Trinity College, Dublin, Ireland
17Kagawaran ng Pediatrics, Indiana University School of Medicine, IUPUI-Wells Center para sa Pediatric Research, Indianapolis, Estados Unidos
18Laboratory of Glycobiology, Hirszfeld Institute of Immunology at Experimental Therapy, Wroclaw, Poland
19BioMarin Pharmaceutical Inc., Novato, Estados Unidos