Mga Highlight Mula sa Ika-62 na Taunang ASH ng Pagpupulong at Paglalahad
AMT-060 Gene Therapy sa Mga Matanda na May Matindi o Katamtamang-Malubhang Hemophilia B Kinumpirma ang Matatag na Ekspresyon ng FIX at Matatag na Pagbawas sa Pagdurugo at Factor IX na Pagkonsumo hanggang sa 5 Taon
Frank WG Leebeek, MD, PhD1, Karina Meijer, MD, PhD2, Michiel Coppens, MD3, Peter Kampmann, MD4, Robert Klamroth, MD, PhD5, Roger Schutgens, MD, PhD, MSc6, Giancarlo Castaman, MD7, Erhard Seifried, MD, PhD8, Joachim Schwaeble9, Halvard Bönig1,10, Eileen KK Sawyer, PhD11, at Wolfgang A. Miesbach, MD12
1Erasmus University Medical Center, Rotterdam, Netherlands
2Dept. ng Hematology, University of Groningen, University Medical Center Groningen, Groningen, Netherlands
3Amsterdam University Medical Center, Unibersidad ng Amsterdam, Amsterdam, Netherlands
4Rigshospitalet, Copenhagen, Denmark
5Kagawaran para sa Panloob na Gamot, Vascular Medicine at Haemostaseology, Vivantes Klinikum im Friedrichshain, Berlin, Germany
6Van Creveldkliniek, University Medical Center Utrecht, Utrecht University, Utrecht, Netherlands
7Azienda Ospedaliera Universitaria Careggi, Florence, Italya
8Institute Frankfurt, Aleman Red Cross Blood Service Baden Wurttemberg-Hessen, Frankfurt, Germany
9Institute Frankfurt, German Red Cross Blood Service Baden-Wurttemberg-Hessen, Frankfurt, Germany
10University of Washington School of Medicine, Seattle, WA
11uniQure Inc., Lexington, MA
12Universitatsklinikum Frankfurt, Frankfurt, Germany
Frank WG Leebeek, MD, PhD1, Karina Meijer, MD, PhD2, Michiel Coppens, MD3, Peter Kampmann, MD4, Robert Klamroth, MD, PhD5, Roger Schutgens, MD, PhD, MSc6, Giancarlo Castaman, MD7, Erhard Seifried, MD, PhD8, Joachim Schwaeble9, Halvard Bönig1,10, Eileen KK Sawyer, PhD11, at Wolfgang A. Miesbach, MD12
1Erasmus University Medical Center, Rotterdam, Netherlands
2Dept. ng Hematology, University of Groningen, University Medical Center Groningen, Groningen, Netherlands
3Amsterdam University Medical Center, Unibersidad ng Amsterdam, Amsterdam, Netherlands
4Rigshospitalet, Copenhagen, Denmark
5Kagawaran para sa Panloob na Gamot, Vascular Medicine at Haemostaseology, Vivantes Klinikum im Friedrichshain, Berlin, Germany
6Van Creveldkliniek, University Medical Center Utrecht, Utrecht University, Utrecht, Netherlands
7Azienda Ospedaliera Universitaria Careggi, Florence, Italya
8Institute Frankfurt, Aleman Red Cross Blood Service Baden Wurttemberg-Hessen, Frankfurt, Germany
9Institute Frankfurt, German Red Cross Blood Service Baden-Wurttemberg-Hessen, Frankfurt, Germany
10University of Washington School of Medicine, Seattle, WA
11uniQure Inc., Lexington, MA
12Universitatsklinikum Frankfurt, Frankfurt, Germany