Mga Highlight Mula sa ika-14 Taunang Kongreso ng EAHAD
Pag-follow up sa isang Novel Adeno-Associated Virus (AAV) Gene Therapy (FLT180a) Pagkamit ng Normal na Mga Antas ng Aktibidad ng FIX sa Malubhang Hemophilia B (HB) Mga Pasyente
(Pag-aaral ng B-AMAZE)
Pratima Chowdary,1,2 Susan Shapiro,3 Mike Makris,4 Gillian Evans,5 Sara Boyce,6 Kausap ni Kate,7 Gerry Dolan,8 Ulrike Reiss,9 Mark Phillips,1,2 Anne Riddell,1 Maria Rita Peralta,1 Michelle Quaye,2 Ted Tuddenham,1 Andrew Smith,10 Alison Long,10 Julie Krop,10 Amit Nathwani1,2
1Katharine Dormandy Haemophilia and Thrombosis Center, Royal Free Hospital, London, UK
2University College London, London, UK
3Oxford Haemophilia Center, Oxford, UK
4Unibersidad ng Sheffield, Sheffield, UK
5Kent at Canterbury Hospital, Canterbury, UK
6University Hospital Southampton, Southampton, UK
7Newcastle Haemophilia Comprehensive Care Center, Newcastle, UK
8St Thomas 'at Guy's Hospital, London, UK
9St Jude Children's Research, Memphis, TN, USA
10Freeline, Stevenage, UK
Pratima Chowdary,1,2 Susan Shapiro,3 Mike Makris,4 Gillian Evans,5 Sara Boyce,6 Kausap ni Kate,7 Gerry Dolan,8 Ulrike Reiss,9 Mark Phillips,1,2 Anne Riddell,1 Maria Rita Peralta,1 Michelle Quaye,2 Ted Tuddenham,1 Andrew Smith,10 Alison Long,10 Julie Krop,10 Amit Nathwani1,2
1Katharine Dormandy Haemophilia and Thrombosis Center, Royal Free Hospital, London, UK
2University College London, London, UK
3Oxford Haemophilia Center, Oxford, UK
4Unibersidad ng Sheffield, Sheffield, UK
5Kent at Canterbury Hospital, Canterbury, UK
6University Hospital Southampton, Southampton, UK
7Newcastle Haemophilia Comprehensive Care Center, Newcastle, UK
8St Thomas 'at Guy's Hospital, London, UK
9St Jude Children's Research, Memphis, TN, USA
10Freeline, Stevenage, UK