Mga Highlight Mula sa 63rd ASH Annual Meeting
Ang Factor IX Expression sa loob ng Normal na Saklaw ay Pinipigilan ang Kusang Pagdurugo na Nangangailangan ng Paggamot Kasunod ng FLT180a Gene Therapy sa Mga Pasyenteng May Malubhang Hemophilia B: Pangmatagalang Follow-up na Pag-aaral ng B-Amaze Program
Pratima Chowdary1,2, Susan Shapiro, MA, BM BCh, FRCP, FRCPath3,4, Mike Makris, MD5, Gillian Evans6, Sara Boyce7, Kate Talks8, Gerry Dolan, MBChB, FRCP, FRCPath9, Ulrike Reiss10 *, Mark Phillips1,2, Anne Riddell1, Maria Rita Peralta1, Michelle Quaye2, Ted Tuddenham1*, Alison Long11, Julie Krop11, at Amit Nathwani, MD, PhD1,2
1Katharine Dormandy Haemophilia and Thrombosis Center, Royal Free Hospital, London, United Kingdom
2University College London, London, United Kingdom
3Mga Ospital ng Unibersidad ng Oxford, Oxford, United Kingdom
4Unibersidad ng Oxford, Oxford, United Kingdom
5Unibersidad ng Sheffield, Sheffield, United Kingdom
6Kent at Canterbury Hospital, Canterbury, United Kingdom
7University Hospital Southampton, Southampton, United Kingdom
8Newcastle Upon Tyne Hospitals NHS Foundation Trust, Newcastle Upon Tyne, GBR
9Haemostasis and Thrombosis Center, Guy's and St Thomas' NHS Foundation Trust, London, United Kingdom
10St Jude Children's Research Hospital, Memphis, TN
11Freeline, Stevenage, United Kingdom