Mga Highlight Mula sa ika-14 Taunang Kongreso ng EAHAD
Etranacogene Dezaparvovec (variant AAV5-Padua hFIX), isang Pinahusay na Vector para sa Paglipat ng Gene sa Mga Matanda na May Malubha o Katamtamang-Malubhang Hemophilia B: Dalawang Taon na Data Mula sa isang Phase 2b Trial
Annette von Drygalski, MD, PharmD1, Adam Giermasz, MD, PhD2, Giancarlo Castaman, MD3, Nigel S. Key, MBChB4, Susan U. Lattimore, RN5, Frank WG Leebeek, MD6, Wolfgang A. Miesbach, MD, PhD7, Michael Recht, MD, PhD5, Esteban Gomez, MD8, Robert Gut, MD, PhD9, at Steven W. Pipe, MD10
1Unibersidad ng California San Diego, La Jolla, CA, USA
2Unibersidad ng California Davis, Sacramento, CA, USA
3Azienda Ospedaliera Universitaria Careggi, Florence, Italya
4Pamantasan ng North Carolina, Chapel Hill, USA
5Oregon Health and Science University, Portland, USA
6Erasmus University Medical Center, Rotterdam, Netherlands
7University Hospital Frankfurt, Alemanya
8Phoenix Children's Hospital, Phoenix, USA
9uniQure Inc, Lexington, MA, USA
10Unibersidad ng Michigan, Ann Arbor, MI, USA
Annette von Drygalski, MD, PharmD1, Adam Giermasz, MD, PhD2, Giancarlo Castaman, MD3, Nigel S. Key, MBChB4, Susan U. Lattimore, RN5, Frank WG Leebeek, MD6, Wolfgang A. Miesbach, MD, PhD7, Michael Recht, MD, PhD5, Esteban Gomez, MD8, Robert Gut, MD, PhD9, at Steven W. Pipe, MD10
1Unibersidad ng California San Diego, La Jolla, CA, USA
2Unibersidad ng California Davis, Sacramento, CA, USA
3Azienda Ospedaliera Universitaria Careggi, Florence, Italya
4Pamantasan ng North Carolina, Chapel Hill, USA
5Oregon Health and Science University, Portland, USA
6Erasmus University Medical Center, Rotterdam, Netherlands
7University Hospital Frankfurt, Alemanya
8Phoenix Children's Hospital, Phoenix, USA
9uniQure Inc, Lexington, MA, USA
10Unibersidad ng Michigan, Ann Arbor, MI, USA