Mga highlight mula sa WFH Virtual Summit 2020
Apat na taong-tao na Pag-aaral ng Pag-follow-up ng Matibay na Kahusayan sa Kalusugan at Kaligtasan: AAV Gene Therapy Sa Valoctocogene Roxaparvovec para sa Malubhang Haemophilia A
K. John Pasi, MB, ChB, PhD, FRCP, FRCPath, FRCPCH1; Savita Rangarajan, MBBS, FRCP, FRCPath2; Nina Mitchell, MB, BChir3; Ang Lester, MB, ChB, PhD, FRCP, FRCPath4; Emily Symington, BSc, MBBS, MRCP, FRCPath5; Bella Madan, MD, FRCP, FRCPath6; Michael Laffan, DM, FRCP, FRCPath7; Chris B. Russell, PhD3; Mingjin Li, MSc3; Benjamin Kim, MD, MPhil3; Glenn F. Pierce, MD, PhD8; Wing Yen Wong, MD3
1Barts at ang London School of Medicine at Dentistry, London, UK
2University Hospital Southampton, Southampton, UK
3BioMarin Pharmaceutical Inc., Novato, CA, USA
4Mga Ospital ng Unibersidad ng Birmingham NHS Foundation Trust, Birmingham, UK
5Mga Ospital ng Cambridge University NHS Foundation Trust, Cambridge, UK
6Guy & St Thomas 'NHS Foundation Trust, London, UK
7Center para sa Hematology, Imperial College London, London, UK.
8Konsulta, La Jolla, CA, USA
K. John Pasi, MB, ChB, PhD, FRCP, FRCPath, FRCPCH1; Savita Rangarajan, MBBS, FRCP, FRCPath2; Nina Mitchell, MB, BChir3; Ang Lester, MB, ChB, PhD, FRCP, FRCPath4; Emily Symington, BSc, MBBS, MRCP, FRCPath5; Bella Madan, MD, FRCP, FRCPath6; Michael Laffan, DM, FRCP, FRCPath7; Chris B. Russell, PhD3; Mingjin Li, MSc3; Benjamin Kim, MD, MPhil3; Glenn F. Pierce, MD, PhD8; Wing Yen Wong, MD3
1Barts at ang London School of Medicine at Dentistry, London, UK
2University Hospital Southampton, Southampton, UK
3BioMarin Pharmaceutical Inc., Novato, CA, USA
4Mga Ospital ng Unibersidad ng Birmingham NHS Foundation Trust, Birmingham, UK
5Mga Ospital ng Cambridge University NHS Foundation Trust, Cambridge, UK
6Guy & St Thomas 'NHS Foundation Trust, London, UK
7Center para sa Hematology, Imperial College London, London, UK.
8Konsulta, La Jolla, CA, USA