Mga highlight mula sa WFH Virtual Summit 2020
Kamakailang Pag-unlad sa Pag-unlad ng AMT-061 (Etranacogene Dezaparvovec) para sa Mga Taong May Matindi o Katamtamang Malubhang Hemophilia B
Steven W. Pipa,1 Wolfgang Miesbach,2 Annette Von Drygalski,3 Adam Giermasz,4 Karina Meijer,5 Michiel Coppens,6 Peter Kampmann,7 Robert Klamroth,8 Roger Schutgens,9 Nigel S. Key,10 Susan Lattimore,11 Michael Recht,12 Esteban Gomez,13 Giancarlo Castaman,14 Eileen K. Sawyer,12 Robert Gut,12 Frank WG Leebeek15
1Unibersidad ng Michigan, Ann Arbor, USA
2University Hospital Frankfurt, Frankfurt, Alemanya
3Pamantasan ng California San Diego, San Diego, USA
4Pamantasan ng California Davis, Sacramento, USA
5University Medical Center Groningen, Groningen, Netherlands
6Akademikong Medical Center, Amsterdam, Ang Netherlands
7Rigshospitalet, Copenhagen, Denmark
8Vivantes Klinikum, Berlin, Germany
9University Medical Center, Utrecht, Netherlands
10Pamantasan ng North Carolina, Chapel Hill, USA
11Oregon Health & Science University, Portland, USA
12uniQure biopharma BV, Lexington, MA, USA
13Ang Hospital sa Bata ng Phoenix, Phoenix USA
14Azienda Ospedaliera Universitaria Careggi, Florence, Italya
15Erasmus University Medical Center, Rotterdam, Netherlands
Steven W. Pipa,1 Wolfgang Miesbach,2 Annette Von Drygalski,3 Adam Giermasz,4 Karina Meijer,5 Michiel Coppens,6 Peter Kampmann,7 Robert Klamroth,8 Roger Schutgens,9 Nigel S. Key,10 Susan Lattimore,11 Michael Recht,12 Esteban Gomez,13 Giancarlo Castaman,14 Eileen K. Sawyer,12 Robert Gut,12 Frank WG Leebeek15
1Unibersidad ng Michigan, Ann Arbor, USA
2University Hospital Frankfurt, Frankfurt, Alemanya
3Pamantasan ng California San Diego, San Diego, USA
4Pamantasan ng California Davis, Sacramento, USA
5University Medical Center Groningen, Groningen, Netherlands
6Akademikong Medical Center, Amsterdam, Ang Netherlands
7Rigshospitalet, Copenhagen, Denmark
8Vivantes Klinikum, Berlin, Germany
9University Medical Center, Utrecht, Netherlands
10Pamantasan ng North Carolina, Chapel Hill, USA
11Oregon Health & Science University, Portland, USA
12uniQure biopharma BV, Lexington, MA, USA
13Ang Hospital sa Bata ng Phoenix, Phoenix USA
14Azienda Ospedaliera Universitaria Careggi, Florence, Italya
15Erasmus University Medical Center, Rotterdam, Netherlands