Mambo muhimu kutoka kwa Bunge la 14 la Mwaka la EAHAD
Fuatilia Tiba ya Jeni ya Adeno-Associated Virus (AAV) Gene Therapy (FLT180a) Kufikia Ngazi za Kawaida za Shughuli za FIX katika Wagonjwa Wakubwa wa Hemophilia B (HB)
(Utafiti wa B-AMAZE)
Ubora wa Pratima,1,2 Susan Shapiro,3 Mike Makris,4 Gillian Evans,5 Sara Boyce,6 Mazungumzo ya Kate,7 Gerry Dolan,8 Ulrike Reiss,9 Mark Phillips,1,2 Anne Riddell,1 Maria Rita Peralta,1 Michelle Quaye,2 Ted Tuddenham,1 Andrew Smith,10 Alison Long,10 Julie Krop,10 Amit Nathwani1,2
1Katharine Dormandy Haemophilia na Kituo cha Thrombosis, Hospitali ya Royal Free, London, Uingereza
2Chuo Kikuu cha London, London, Uingereza
3Kituo cha Oxford Haemophilia, Oxford, Uingereza
4Chuo Kikuu cha Sheffield, Sheffield, Uingereza
5Hospitali ya Kent na Canterbury, Canterbury, Uingereza
6Hospitali ya Chuo Kikuu Southampton, Southampton, Uingereza
7Kituo cha Huduma ya kina cha Newcastle Haemophilia, Newcastle, Uingereza
8Hospitali ya St Thomas 'na Guy, London, Uingereza
9Utafiti wa Watoto wa St Jude, Memphis, TN, USA
10Freeline, Stevenage, Uingereza
Ubora wa Pratima,1,2 Susan Shapiro,3 Mike Makris,4 Gillian Evans,5 Sara Boyce,6 Mazungumzo ya Kate,7 Gerry Dolan,8 Ulrike Reiss,9 Mark Phillips,1,2 Anne Riddell,1 Maria Rita Peralta,1 Michelle Quaye,2 Ted Tuddenham,1 Andrew Smith,10 Alison Long,10 Julie Krop,10 Amit Nathwani1,2
1Katharine Dormandy Haemophilia na Kituo cha Thrombosis, Hospitali ya Royal Free, London, Uingereza
2Chuo Kikuu cha London, London, Uingereza
3Kituo cha Oxford Haemophilia, Oxford, Uingereza
4Chuo Kikuu cha Sheffield, Sheffield, Uingereza
5Hospitali ya Kent na Canterbury, Canterbury, Uingereza
6Hospitali ya Chuo Kikuu Southampton, Southampton, Uingereza
7Kituo cha Huduma ya kina cha Newcastle Haemophilia, Newcastle, Uingereza
8Hospitali ya St Thomas 'na Guy, London, Uingereza
9Utafiti wa Watoto wa St Jude, Memphis, TN, USA
10Freeline, Stevenage, Uingereza