Mambo muhimu kutoka kwa Mkutano Mkuu wa WFH 2020
Utafiti wa ufuatiliaji wa miaka ya kwanza wa mwanadamu wa Utabiri wa kudumu wa matibabu na Usalama: Tiba ya AAV Gene Na Valoctocogene Roxaparvovec ya Severe Haemophilia A
K. John Pasi, MB, ChB, PhD, FRCP, FRCPath, FRCPCH1; Savita Rangarajan, MBBS, FRCP, FRCPath2; Nina Mitchell, MB, BChir3; Je Lester, MB, ChB, PhD, FRCP, FRCPath4; Emily Symington, BSc, MBBS, MRCP, FRCPath5; Bella Madan, MD, FRCP, FRCPath6; Michael Laffan, DM, FRCP, FRCPath7; Chris B. Russell, PhD3; Mingjin Li, MSc3; Benjamin Kim, MD, MPhil3; Glenn F. Pierce, MD, PhD8; Mrengo Yen Wong, MD3
1Barts na Shule ya London ya Tiba na meno, London, Uingereza
2Hospitali ya Chuo Kikuu Southampton, Southampton, Uingereza
3Inc ya BioMarin Madawa Inc, Novato, CA, USA
4Hospitali za Chuo Kikuu cha Birmingham NHS Trust Trust, Birmingham, Uingereza
5Hospitali ya Chuo Kikuu cha Cambridge NHS Foundation Trust, Cambridge, Uingereza
6Guy's & St. Thomas 'NHS Foundation Trust, London, Uingereza
7Kituo cha Hematolojia, Chuo cha Imperi London, London, Uingereza.
8Mshauri, La Jolla, CA, USA
K. John Pasi, MB, ChB, PhD, FRCP, FRCPath, FRCPCH1; Savita Rangarajan, MBBS, FRCP, FRCPath2; Nina Mitchell, MB, BChir3; Je Lester, MB, ChB, PhD, FRCP, FRCPath4; Emily Symington, BSc, MBBS, MRCP, FRCPath5; Bella Madan, MD, FRCP, FRCPath6; Michael Laffan, DM, FRCP, FRCPath7; Chris B. Russell, PhD3; Mingjin Li, MSc3; Benjamin Kim, MD, MPhil3; Glenn F. Pierce, MD, PhD8; Mrengo Yen Wong, MD3
1Barts na Shule ya London ya Tiba na meno, London, Uingereza
2Hospitali ya Chuo Kikuu Southampton, Southampton, Uingereza
3Inc ya BioMarin Madawa Inc, Novato, CA, USA
4Hospitali za Chuo Kikuu cha Birmingham NHS Trust Trust, Birmingham, Uingereza
5Hospitali ya Chuo Kikuu cha Cambridge NHS Foundation Trust, Cambridge, Uingereza
6Guy's & St. Thomas 'NHS Foundation Trust, London, Uingereza
7Kituo cha Hematolojia, Chuo cha Imperi London, London, Uingereza.
8Mshauri, La Jolla, CA, USA