Höjdpunkter från det 62: e ASH-årsmötet och utställningen
Uppdaterad uppföljning av Alta-studien, en fas 1/2-studie av giroktokogen Fitelparvovec (SB-525) Genterapi hos vuxna med svår hemofili A
Andrew D. Leavitt, MD1Barbara A. Konkle, MD2,3, Kimo Stine, MD4, Nathan Visweshwar, MD5Thomas J. Harrington, MD6Adam Giermasz, MD, doktor7, Steven Arkin, MD8, Annie Fang, MD, doktor9Frank Plonski, RN, MA8, Lynne Smith, MBA10, Li-Jung Tseng, doktorsexamen, MBA9, Gregory Di Russo, MD8, Bettina M Cockroft, MD11, Jeremy Rupon, MD10 och Didier Rouy, läkare, doktorsexamen11
1University of California, San Francisco, CA
2University of Washington, Seattle, WA
3University of Washington, Washington Center for Bleeding Disorders, Seattle, WA
4UAMS vid Arkansas Children's Hospital, Little Rock, AR
5University of South Florida, Tampa, FL
6University of Miami Miller School of Medicine, Miami, FL
7University of California Davis, Sacramento, CA
8Pfizer Inc, Cambridge, MA
9Pfizer Inc, New York, NY
10Pfizer Inc, Collegeville, PA
11Sangamo Therapeutics, Brisbane, CA
Andrew D. Leavitt, MD1Barbara A. Konkle, MD2,3, Kimo Stine, MD4, Nathan Visweshwar, MD5Thomas J. Harrington, MD6Adam Giermasz, MD, doktor7, Steven Arkin, MD8, Annie Fang, MD, doktor9Frank Plonski, RN, MA8, Lynne Smith, MBA10, Li-Jung Tseng, doktorsexamen, MBA9, Gregory Di Russo, MD8, Bettina M Cockroft, MD11, Jeremy Rupon, MD10 och Didier Rouy, läkare, doktorsexamen11
1University of California, San Francisco, CA
2University of Washington, Seattle, WA
3University of Washington, Washington Center for Bleeding Disorders, Seattle, WA
4UAMS vid Arkansas Children's Hospital, Little Rock, AR
5University of South Florida, Tampa, FL
6University of Miami Miller School of Medicine, Miami, FL
7University of California Davis, Sacramento, CA
8Pfizer Inc, Cambridge, MA
9Pfizer Inc, New York, NY
10Pfizer Inc, Collegeville, PA
11Sangamo Therapeutics, Brisbane, CA