Highlights From the ASGCT 25th Annual Meeting
Stable Hemostatic Correction and Improved Hemophilia-Related Quality of Life: Final Analysis from the Pivotal Phase 3 HOPE-B Trial of Etranacogene Dezaparvovec
Presented by: Steven W. Pipe, MD, University of Michigan, Ann Arbor, Michigan, United States
Steven W. Pipe1, Frank W. G. Leebeek2, Michael Recht3, Nigel S. Key4, Giancarlo Castaman5, David Cooper6, Robert Gut6, Ricardo Dolmetsch6, Yanyan Li7, Paul E. Monahan7, Wolfgang Miesbach8
1University of Michigan, Ann Arbor, MI
2Erasmus MC, University Medical Center, Rotterdam, Netherlands
3Oregon Health & Science University, Portland, OR
4University of North Carolina, Chapel Hill, NC
5Center for Bleeding Disorders and Coagulation, Careggi University Hospital, Florence, Italy
6uniQure Inc., Lexington, MA
7CSL Behring, King of Prussia, PA
8University Hospital Frankfurt, Frankfurt, Germany
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