World Federation of Hemophilia Genterapy Registry

Barbara A. Konkle, MD^1,2, Donna Coffin, MSc³, Mayss Naccache¹, Robert Clark⁴, Lindsey George, MD⁵, Alfonso Iorio, MD, PhD⁶, Wolfgang A. Miesbach, MD⁷, Brian O'Mahony⁸, Flora Peyvandi^9,10, Steven W. Pipe, MD¹¹, Adrian Quartel¹², Eileen K Sawyer, PhD¹³, Mark W Skinner, JD¹⁴, Bartholomew J. Tortella, MD, MBA¹⁵, Crystal Watson, BS¹⁶, Leonard A. Valentino, MD¹⁷, Ian Winburn¹⁸, Johnny Mahlangu¹⁹og Glenn F. Pierce, MD, PhD²⁰

¹Verdensføderasjonen for hemofili, Montreal, QC, Canada

²University of Washington, Washington Center for Bleeding Disorders, Seattle, WA

³Verdensføderasjonen for hemofili, Montréal, QC, Canada

⁴International Society on Thrombosis and Hemostasis, Inc, Carrboro

⁵Barnas sykehus i Philadelphia, Philadelphia, PA

⁶McMaster University, Ontario, Canada

⁷Hemophilia Center, Universitetssykehus Frankfurt, Frankfurt, Tyskland

⁸Irish Haemophilia Society, Dublin, Irland

⁹Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Fondazione IRCCS Ca 'Granda Ospedale Maggiore Policlinico, Milano, Italia

¹⁰Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Fondazione IRCCS Ca 'Granda Ospedale Maggiore Policlinico, Milano, Italia

¹¹Pediatri og patologi, University of Michigan, Ann Arbor, MI

¹²BioMarin Pharmaceutical Inc, Novato

¹³uniQure Inc, Lexington, MA

¹⁴Institute for Policy Advancement Ltd, Washington, DC

¹⁵Spark Therapeutics, Philadelphia, PA

¹⁶American Thrombosis and Hemostasis Network, Decatur, GA

¹⁷National Hemophilia Foundation (NHF), New York

¹⁸Pfizer Inc, New York

¹⁹Haemophilia Comprehensive Care Center, Faculty of Health Sciences, University of the Witwatersrand and NHLS, Johannesburg North, Sør-Afrika

²⁰World Federation of Hemophilia, La Jolla, CA