The Impact of Pre-Existing Immunity on the Non-Clinical Pharmacodynamics of AAV5-Based Gene Therapy
ISTH Announces Launch of New Global Education Initiative in Gene Therapy For Hemophilia
Hyperactivity of Factor IX Padua (R338L) Depends on Factor VIIIa Cofactor Activity
How to Discuss Gene Therapy for Haemophilia? A Patient and Physician Perspective