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Immunoadsorption enables successful rAAV5-mediated repeated hepatic gene delivery in nonhuman primates

Immunoadsorption enables successful rAAV5-mediated repeated hepatic gene delivery in nonhuman primates

28 October 2019

Therapeutic hFIX Activity Achieved After Single AAV5-hFIX Treatment in Hemophilia B Patients and NHPs with Pre-existing Anti-AAV5 NABs

Therapeutic hFIX Activity Achieved After Single AAV5-hFIX Treatment in Hemophilia B Patients and NHPs with Pre-existing Anti-AAV5 NABs

12 August 2019

Science Translational Medicine (05/22/19) Vol. 11, No. 493 Milani, Michela; Annoni, Andrea; Moalli, Federica; et al.

Clinical Advances in Gene Therapy Updates on Clinical Trials of Gene Therapy in Haemophilia

Clinical Advances in Gene Therapy Updates on Clinical Trials of Gene Therapy in Haemophilia

12 August 2019

Science Translational Medicine (05/22/19) Vol. 11, No. 493 Milani, Michela; Annoni, Andrea; Moalli, Federica; et al.

The Impact of Pre-Existing Immunity on the Non-Clinical Pharmacodynamics of AAV5-Based Gene Therapy

The Impact of Pre-Existing Immunity on the Non-Clinical Pharmacodynamics of AAV5-Based Gene Therapy

12 August 2019

Science Translational Medicine (05/22/19) Vol. 11, No. 493 Milani, Michela; Annoni, Andrea; Moalli, Federica; et al.

Hyperactivity of Factor IX Padua (R338L) Depends on Factor VIIIa Cofactor Activity
12 August 2019
ISTH Announces Launch of New Global Education Initiative in Gene Therapy For Hemophilia
05 July 2019
How to Discuss Gene Therapy for Haemophilia? A Patient and Physician Perspective
30 June 2019
Adenovirus-Associated Antibodies in UK Cohort of Hemophilia Patients
30 June 2019

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Supported by educational grants from BioMarin, Freeline Therapeutics Limited, Pfizer Inc., Shire, Spark Therapeutics, and uniQure, Inc

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