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Home
About
Roadmap
Steering Committee
About ISTH
Blog
Topics
Basics of Hemophilia
Fundamental of Gene Therapies
Practical Considerations of Gene Therapies
Clinical Trial Efficacy and Safety
Patient Journey: Implementation to Lived Experience
Clinical Perspectives/Real-World Evidence
Roles of the Multidisciplinary Team
Recent Updates and Ongoing Efforts
Education
Resources Builder
Shared Decision Making
HTC Case Studies
EXPLORE Modules
Illustrated Clinical Trials
Interactive Webinars
Podcasts
Roadmap
Gene Therapy Resources
Conference Coverage
Microlearning
Monthly Roundup
News
Learning Tiers
Introductory
Intermediate
Advanced
Home
About
Roadmap
Steering Committee
About ISTH
Blog
Topics
Basics of Hemophilia
Fundamental of Gene Therapies
Practical Considerations of Gene Therapies
Clinical Trial Efficacy and Safety
Patient Journey: Implementation to Lived Experience
Clinical Perspectives/Real-World Evidence
Roles of the Multidisciplinary Team
Recent Updates and Ongoing Efforts
Education
Resources Builder
Shared Decision Making
HTC Case Studies
EXPLORE Modules
Illustrated Clinical Trials
Interactive Webinars
Podcasts
Roadmap
Gene Therapy Resources
Conference Coverage
Microlearning
Monthly Roundup
News
Learning Tiers
Introductory
Intermediate
Advanced
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Latest News
The WFH Guidelines for the Management of Haemophilia: AAV Gene Therapy, 2025
25 October 2025
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Gene therapy for hemophilia: results of ISTH global survey on current knowledge, attitudes, and preparedness of the hemophilia care team
22 October 2025
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Results from the BENEGENE-2 trial
17 October 2025
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Comparative Effectiveness of Valoctocogene Roxaparvovec and Efanesoctocog Alfa in the Treatment of Severe Hemophilia A: A Matching-Adjusted Indirect Comparison of Bleeding Frequency
09 September 2025
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A Precision Gene Engineered B Cell Medicine Producing Sustained Levels of Active Factor IX for Hemophilia B Therapy
05 September 2025
AAV Gene Therapy in Severe Hemophilia B
20 August 2025
Children’s Hospital Administers First Commercially Available Gene Therapy for Hemophilia B
06 August 2025
Why is the uptake of gene therapy in hemophilia less than expected?
22 July 2025
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Supported through educational grants from BioMarin, CSL Behring, Pfizer Inc., Roche, and Spark Therapeutics
Home
About
Roadmap
Steering Committee
About ISTH
Blog
Topics
Basics of Hemophilia
Fundamental of Gene Therapies
Practical Considerations of Gene Therapies
Clinical Trial Efficacy and Safety
Patient Journey: Implementation to Lived Experience
Clinical Perspectives/Real-World Evidence
Roles of the Multidisciplinary Team
Recent Updates and Ongoing Efforts
Education
Resources Builder
Shared Decision Making
HTC Case Studies
EXPLORE Modules
Illustrated Clinical Trials
Interactive Webinars
Podcasts
Roadmap
Gene Therapy Resources
Conference Coverage
Microlearning
Monthly Roundup
News
Learning Tiers
Introductory
Intermediate
Advanced
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