Multiyear Follow-up of AAV5-hFVIII-SQ Gene Therapy for Hemophilia A

Multiyear Follow-up of AAV5-hFVIII-SQ Gene Therapy for Hemophilia A

Pasi KJ, et al. N Engl J Med. 2020 Jan 2;382(1):29-40. doi: 10.1056/NEJMoa1908490.