Gene Therapy Latest News | Experimental Gene Therapy Studies

Hemophilia B Gene Therapy AMT-061 Unlikely to Have Caused Liver Tumor

01 April 2021

Gene Therapy SPK-8016 Shows Early Promise for Severe Hemophilia A

08 February 2021

Roctavian, Potential Hemophilia A Gene Therapy, Get Fresh FDA Support

11 March 2021

Roctavian, Hem A Gene Therapy, Sustains Drop in Bleeding Rates, Phase 3 Data Show

13 January 2021

BioMarin Announces Positive Phase 3 Gene Therapy Trial Results in Adults with Severe Hemophilia A; Study Met All Primary and Secondary Efficacy Endpoints in One-Year Data Set
10 January 2021
Non-viral Gene Therapy Shows Promise in Hemophilia A Animal Models
06 January 2021
Freeline Reports Updated Data From Phase 1/2 B-AMAZE Trial in Hemophilia B
14 December 2020
UniQure Shares Long-term Data About AMT-061 and AMT-060 Gene Therapy Candidates
09 December 2020

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Supported by educational grants from BioMarin, Freeline Therapeutics Limited, Pfizer Inc., Shire, Spark Therapeutics, and uniQure, Inc

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