Punti Ewlenin Mill-14-il Kungress Annwali tal-EAHAD
Segwitu ta 'Terapija tal-Ġeni ta' Virus Ġdid Assoċjat ma 'Adeno (AAV) (FLT180a) Kisba ta' Livelli ta 'Attività FIX Normali f'Pazjenti ta' Emofilja B Severa (HB)
(Studju B-AMAZE)
Pratima Chowdary,1,2 Susan Shapiro,3 Mike Makris,4 Gillian Evans,5 Sara Boyce,6 Kate Taħdidiet,7 Gerry Dolan,8 Ulrike Reiss,9 Mark Phillips,1,2 Anne Riddell,1 Maria Rita Peralta,1 Michelle Quaye,2 Ted Tuddenham,1 Andrew Smith,10 Alison Long,10 Julie Krop,10 Amit Nathwani1,2
1Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free Hospital, Londra, ir-Renju Unit
2University College London, Londra, UK
3Oxford Haemophilia Centre, Oxford, ir-Renju Unit
4Università ta 'Sheffield, Sheffield, ir-Renju Unit
5Kent u l-Isptar Canterbury, Canterbury, ir-Renju Unit
6Sptar Universitarju ta ’Southampton, Southampton, ir-Renju Unit
7Newcastle Haemophilia Comprehensive Care Centre, Newcastle, ir-Renju Unit
8St Thomas 'and Guy's Hospital, Londra, ir-Renju Unit
9St Jude Children's Research, Memphis, TN, USA
10Freeline, Stevenage, ir-Renju Unit
Pratima Chowdary,1,2 Susan Shapiro,3 Mike Makris,4 Gillian Evans,5 Sara Boyce,6 Kate Taħdidiet,7 Gerry Dolan,8 Ulrike Reiss,9 Mark Phillips,1,2 Anne Riddell,1 Maria Rita Peralta,1 Michelle Quaye,2 Ted Tuddenham,1 Andrew Smith,10 Alison Long,10 Julie Krop,10 Amit Nathwani1,2
1Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free Hospital, Londra, ir-Renju Unit
2University College London, Londra, UK
3Oxford Haemophilia Centre, Oxford, ir-Renju Unit
4Università ta 'Sheffield, Sheffield, ir-Renju Unit
5Kent u l-Isptar Canterbury, Canterbury, ir-Renju Unit
6Sptar Universitarju ta ’Southampton, Southampton, ir-Renju Unit
7Newcastle Haemophilia Comprehensive Care Centre, Newcastle, ir-Renju Unit
8St Thomas 'and Guy's Hospital, Londra, ir-Renju Unit
9St Jude Children's Research, Memphis, TN, USA
10Freeline, Stevenage, ir-Renju Unit