Punti Ewlenin Mill-15-il Kungress Annwali tal-EAHAD
Impatt tat-Trasferiment tal-Ġene Valoctocogene Roxaparvovec għal Emofilja A Severa fuq il-Kwalità tal-Ħajja relatata mas-Saħħa
B.O'Mahony1,2; J.Mahlangu3; K.Peerlinck4; JDWang5; G.Lowe6; CWTan7; A.Giermasz8; H.Tran9; TLKhoo10; E.Cockrell11; D.Pepperell12; H.Chambost13; MFLernández14; R.Kazmi15; E.Majerus16; MWSkinner17,18; R.Klamroth19; J.Quinn20; H.Yu20; WYWong20; A.Lawal20; TMRobinson20; B.Kim20
1Soċjetà Irlandiża tal-Emofilja;2Trinity College, Dublin, l-Irlanda;3 Emophilia Comprehensive Care Center, Charlotte Maxeke Johannesburg Academic Hospital, University of the Witwatersrand u NHLS, Johannesburg, Afrika t'Isfel;4 Dipartiment tal-Mediċina Vaskulari u Emostasi u Emofilja Ċentru, Sptarijiet Universitarji Leuven, Leuven, il-Belġju;5 Centerfor Rare Disease and Hemophilia, Taichung Veterans General Hospital, Taichung, Tajwan, Provinċja taċ-Ċina;6 West Midlands Comprehensive Care Haemophilia Centre, Queen Elizabeth Hospital, Birmingham, ir-Renju Unit;7 Dipartiment tal-Ematoloġija, Royal Adelaide Hospital, Adelaide, l-Awstralja;8 Ċentru ta 'Trattament tal-Emofilja, Università ta' California Davis, Sacramento, l-Istati Uniti;9 Haemostasis & Thrombosis Unit, Emophilia Treatment Centre, The Alfred Hospital, Melbourne;10 Istitut tal-Ematoloġija, Royal Prince Alfred Hospital, Camperdown, l-Awstralja;11 Onkoloġija tal-Ematoloġija Pedjatrika, Saint Joseph's Children's Hospital, Tampa, l-Istati Uniti;12 Dipartiment tal-Ematoloġija, Fiona Stanley Hospital, Murdoch, l-Awstralja;13 AP-HM, Dipartiment tal-Onkoloġija tal-Ematoloġija Pedjatrika, l-Isptar tat-Tfal La Timone, Università ta 'Aix Marseille, INSERM, INRA, C2VN, Marsilja, Franza;14 Complejo Hospitalario Universitario A Coruña, A Coruña, Spanja;15 Dipartiment tal-Ematoloġija, Southampton University Hospital, Southampton, ir-Renju Unit;16 Dipartiment tal-Mediċina, Washington University f'St Louis, St.17 Institute for Policy Advancement Ltd, Washington, l-Istati Uniti;18 McMaster University, Hamilton, Kanada;19 Ċentru għat-Trattament tal-Emofilja tal-Kura Komprensiva, Vivantes Klinikumim Friedrichshain, Berlin, il-Ġermanja;20 BioMarin Pharmaceutical Inc., Novato, l-Istati Uniti