Punti ewlenin mis-Samit Virtwali WFH 2020
Studju ta 'Segwitu ta' erba 'snin fil-bniedem għall-Effiċjenza u s-Sigurtà Terapewtika Durabbli: Terapija tal-Ġeni AAV B'Valoctocogene Roxaparvovec għal Emofilja Severa A
K. John Pasi, MB, ChB, PhD, FRCP, FRCPath, FRCPCH1; Savita Rangarajan, MBBS, FRCP, FRCPath2; Nina Mitchell, MB, BChir3; Lester Will, MB, ChB, PhD, FRCP, FRCPath4; Emily Symington, BSc, MBBS, MRCP, FRCPath5; Bella Madan, MD, FRCP, FRCPath6; Michael Laffan, DM, FRCP, FRCPath7; Chris B. Russell, PhD3; Mingjin Li, MSc3; Benjamin Kim, MD, MPhil3; Glenn F. Pierce, MD, PhD8; Wing Yen Wong, MD3
1Barts u l-Iskola ta 'Mediċina u Dentistrija ta' Londra, Londra, ir-Renju Unit
2Sptar Universitarju ta ’Southampton, Southampton, ir-Renju Unit
3BioMarin Pharmaceutical Inc., Novato, CA, l-Istati Uniti
4Sptarijiet Universitarji ta ’Birmingham NHS Foundation Trust, Birmingham, ir-Renju Unit
5Sptarijiet tal-Università ta ’Cambridge NHS Foundation Foundation, Cambridge, ir-Renju Unit
6Guy's & St Thomas 'NHS Foundation Trust, Londra, ir-Renju Unit
7Ċentru għall-Ematoloġija, Imperial College London, Londra, ir-Renju Unit.
8Konsulent, La Jolla, CA, USA
K. John Pasi, MB, ChB, PhD, FRCP, FRCPath, FRCPCH1; Savita Rangarajan, MBBS, FRCP, FRCPath2; Nina Mitchell, MB, BChir3; Lester Will, MB, ChB, PhD, FRCP, FRCPath4; Emily Symington, BSc, MBBS, MRCP, FRCPath5; Bella Madan, MD, FRCP, FRCPath6; Michael Laffan, DM, FRCP, FRCPath7; Chris B. Russell, PhD3; Mingjin Li, MSc3; Benjamin Kim, MD, MPhil3; Glenn F. Pierce, MD, PhD8; Wing Yen Wong, MD3
1Barts u l-Iskola ta 'Mediċina u Dentistrija ta' Londra, Londra, ir-Renju Unit
2Sptar Universitarju ta ’Southampton, Southampton, ir-Renju Unit
3BioMarin Pharmaceutical Inc., Novato, CA, l-Istati Uniti
4Sptarijiet Universitarji ta ’Birmingham NHS Foundation Trust, Birmingham, ir-Renju Unit
5Sptarijiet tal-Università ta ’Cambridge NHS Foundation Foundation, Cambridge, ir-Renju Unit
6Guy's & St Thomas 'NHS Foundation Trust, Londra, ir-Renju Unit
7Ċentru għall-Ematoloġija, Imperial College London, Londra, ir-Renju Unit.
8Konsulent, La Jolla, CA, USA