Sorotan Dari Kongres Tahunan ke-14 EAHAD
Tindak lanjut Terapi Gen Virus Adeno-Associated (AAV) (FLT180a) Mencapai Tahap Aktiviti FIX Normal pada Pesakit Hemofilia B (HB) yang teruk
(Kajian B-AMAZE)
Pratima Chowdary,1,2 Susan Shapiro,3 Mike Makris,4 Gillian Evans,5 Sara Boyce,6 Ceramah Kate,7 Gerry Dolan,8 Ulrike Reiss,9 Mark Phillips,1,2 Anne Riddell,1 Maria Rita Peralta,1 Michelle Quaye,2 Ted Tuddenham,1 Andrew Smith,10 Alison Long,10 Julie Krop,10 Amit Nathwani1,2
1Katharine Dormandy Haemophilia and Thrombosis Center, Royal Free Hospital, London, UK
2Kolej Universiti London, London, UK
3Pusat Haemophilia Oxford, Oxford, UK
4Universiti Sheffield, Sheffield, UK
5Hospital Kent dan Canterbury, Canterbury, UK
6Hospital Universiti Southampton, Southampton, UK
7Pusat Rawatan Komprehensif Newcastle Haemophilia, Newcastle, UK
8St Thomas 'dan Guy's Hospital, London, UK
9Penyelidikan Kanak-kanak St Jude, Memphis, TN, Amerika Syarikat
10Talian Bebas, Stevenage, UK
Pratima Chowdary,1,2 Susan Shapiro,3 Mike Makris,4 Gillian Evans,5 Sara Boyce,6 Ceramah Kate,7 Gerry Dolan,8 Ulrike Reiss,9 Mark Phillips,1,2 Anne Riddell,1 Maria Rita Peralta,1 Michelle Quaye,2 Ted Tuddenham,1 Andrew Smith,10 Alison Long,10 Julie Krop,10 Amit Nathwani1,2
1Katharine Dormandy Haemophilia and Thrombosis Center, Royal Free Hospital, London, UK
2Kolej Universiti London, London, UK
3Pusat Haemophilia Oxford, Oxford, UK
4Universiti Sheffield, Sheffield, UK
5Hospital Kent dan Canterbury, Canterbury, UK
6Hospital Universiti Southampton, Southampton, UK
7Pusat Rawatan Komprehensif Newcastle Haemophilia, Newcastle, UK
8St Thomas 'dan Guy's Hospital, London, UK
9Penyelidikan Kanak-kanak St Jude, Memphis, TN, Amerika Syarikat
10Talian Bebas, Stevenage, UK