Sorotan Daripada Mesyuarat Tahunan ASH ke-63
Ekspresi Faktor IX Dalam Julat Normal Mencegah Pendarahan Spontan Memerlukan Rawatan Mengikuti Terapi Gen FLT180a pada Pesakit Hemofilia B Teruk: Kajian Susulan Jangka Panjang Program B-Amaze
Pratima Chowdary1,2, Susan Shapiro, MA, BM BCh, FRCP, FRCPath3,4, Mike Makris, MD5, Gillian Evans6, Sara Boyce7, Kate Talks8, Gerry Dolan, MBChB, FRCP, FRCPath9, Ulrike Reiss10 *, Mark Phillips1,2, Anne Riddell1, Maria Rita Peralta1, Michelle Quaye2, Ted Tuddenham1*, Alison Long11, Julie Krop11, dan Amit Nathwani, MD, PhD1,2
1Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free Hospital, London, United Kingdom
2Kolej Universiti London, London, United Kingdom
3Hospital Universiti Oxford, Oxford, United Kingdom
4Universiti Oxford, Oxford, United Kingdom
5Universiti Sheffield, Sheffield, United Kingdom
6Hospital Kent dan Canterbury, Canterbury, United Kingdom
7Hospital Universiti Southampton, Southampton, United Kingdom
8Yayasan NHS Hospital Newcastle Upon Tyne, Newcastle Upon Tyne, GBR
9Pusat Haemostasis dan Trombosis, Guy's and St Thomas' NHS Foundation Trust, London, United Kingdom
10Hospital Penyelidikan Kanak-kanak St Jude, Memphis, TN
11Talian Bebas, Stevenage, United Kingdom