Highlights From the 62nd ASH Annual Meeting and Exposition
Updated Follow-up of the Alta Study, a Phase 1/2 Study of Giroctocogene Fitelparvovec (SB-525) Gene Therapy in Adults With Severe Hemophilia A
Andrew D. Leavitt, MD1, Barbara A. Konkle, MD2,3, Kimo Stine, MD4, Nathan Visweshwar, MD5, Thomas J. Harrington, MD6, Adam Giermasz, MD, PhD7, Steven Arkin, MD8, Annie Fang, MD, PhD9, Frank Plonski, RN, MA8, Lynne Smith, MBA10, Li-Jung Tseng, PhD, MBA9, Gregory Di Russo, MD8, Bettina M Cockroft, MD11, Jeremy Rupon, MD10 and Didier Rouy, MD, PhD11
1University of California, San Francisco, CA
2University of Washington, Seattle, WA
3University of Washington, Washington Center for Bleeding Disorders, Seattle, WA
4UAMS at Arkansas Children's Hospital, Little Rock, AR
5University of South Florida, Tampa, FL
6University of Miami Miller School of Medicine, Miami, FL
7University of California Davis, Sacramento, CA
8Pfizer Inc, Cambridge, MA
9Pfizer Inc, New York, NY
10Pfizer Inc, Collegeville, PA
11Sangamo Therapeutics, Brisbane, CA
Andrew D. Leavitt, MD1, Barbara A. Konkle, MD2,3, Kimo Stine, MD4, Nathan Visweshwar, MD5, Thomas J. Harrington, MD6, Adam Giermasz, MD, PhD7, Steven Arkin, MD8, Annie Fang, MD, PhD9, Frank Plonski, RN, MA8, Lynne Smith, MBA10, Li-Jung Tseng, PhD, MBA9, Gregory Di Russo, MD8, Bettina M Cockroft, MD11, Jeremy Rupon, MD10 and Didier Rouy, MD, PhD11
1University of California, San Francisco, CA
2University of Washington, Seattle, WA
3University of Washington, Washington Center for Bleeding Disorders, Seattle, WA
4UAMS at Arkansas Children's Hospital, Little Rock, AR
5University of South Florida, Tampa, FL
6University of Miami Miller School of Medicine, Miami, FL
7University of California Davis, Sacramento, CA
8Pfizer Inc, Cambridge, MA
9Pfizer Inc, New York, NY
10Pfizer Inc, Collegeville, PA
11Sangamo Therapeutics, Brisbane, CA