Highlights From the 62nd ASH Annual Meeting and Exposition
The World Federation of Hemophilia Gene Therapy Registry
Barbara A. Konkle, MD1,2, Donna Coffin, MSc3, Mayss Naccache1, Robert Clark4, Lindsey George, MD5, Alfonso Iorio, MD, PhD6, Wolfgang A. Miesbach, MD7, Brian O'Mahony8, Flora Peyvandi9,10, Steven W. Pipe, MD11, Adrian Quartel12, Eileen K Sawyer, PhD13, Mark W Skinner, JD14, Bartholomew J. Tortella, MD, MBA15, Crystal Watson, BS16, Leonard A. Valentino, MD17, Ian Winburn18, Johnny Mahlangu19, and Glenn F. Pierce, MD, PhD20
1World Federation of Hemophilia, Montreal, QC, Canada
2University of Washington, Washington Center for Bleeding Disorders, Seattle, WA
3World Federation of Hemophilia, Montréal, QC, Canada
4International Society on Thrombosis and Haemostasis, Inc, Carrboro
5The Children’s Hospital of Philadelphia, Philadelphia, PA
6McMaster University, Ontario, Canada
7Hemophilia Centre, University Hospital Frankfurt, Frankfurt, Germany
8Irish Haemophilia Society, Dublin, Ireland
9Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Fondazione IRCCS Ca’ Granda Ospedale Maggiore Policlinico, Milan, Italy
10Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan, Italy
11Pediatrics and Pathology, University of Michigan, Ann Arbor, MI
12BioMarin Pharmaceutical Inc, Novato
13uniQure Inc, Lexington, MA
14Institute for Policy Advancement Ltd, Washington, DC
15Spark Therapeutics, Philadelphia, PA
16American Thrombosis and Hemostasis Network, Decatur, GA
17National Hemophilia Foundation (NHF), New York
18Pfizer Inc, New York
19Haemophilia Comprehensive Care Centre, Faculty of Health Sciences, University of the Witwatersrand and NHLS, Johannesburg North, South Africa
20World Federation of Hemophilia, La Jolla, CA
Barbara A. Konkle, MD1,2, Donna Coffin, MSc3, Mayss Naccache1, Robert Clark4, Lindsey George, MD5, Alfonso Iorio, MD, PhD6, Wolfgang A. Miesbach, MD7, Brian O'Mahony8, Flora Peyvandi9,10, Steven W. Pipe, MD11, Adrian Quartel12, Eileen K Sawyer, PhD13, Mark W Skinner, JD14, Bartholomew J. Tortella, MD, MBA15, Crystal Watson, BS16, Leonard A. Valentino, MD17, Ian Winburn18, Johnny Mahlangu19, and Glenn F. Pierce, MD, PhD20
1World Federation of Hemophilia, Montreal, QC, Canada
2University of Washington, Washington Center for Bleeding Disorders, Seattle, WA
3World Federation of Hemophilia, Montréal, QC, Canada
4International Society on Thrombosis and Haemostasis, Inc, Carrboro
5The Children’s Hospital of Philadelphia, Philadelphia, PA
6McMaster University, Ontario, Canada
7Hemophilia Centre, University Hospital Frankfurt, Frankfurt, Germany
8Irish Haemophilia Society, Dublin, Ireland
9Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Fondazione IRCCS Ca’ Granda Ospedale Maggiore Policlinico, Milan, Italy
10Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan, Italy
11Pediatrics and Pathology, University of Michigan, Ann Arbor, MI
12BioMarin Pharmaceutical Inc, Novato
13uniQure Inc, Lexington, MA
14Institute for Policy Advancement Ltd, Washington, DC
15Spark Therapeutics, Philadelphia, PA
16American Thrombosis and Hemostasis Network, Decatur, GA
17National Hemophilia Foundation (NHF), New York
18Pfizer Inc, New York
19Haemophilia Comprehensive Care Centre, Faculty of Health Sciences, University of the Witwatersrand and NHLS, Johannesburg North, South Africa
20World Federation of Hemophilia, La Jolla, CA