Highlights From the 30th Congress of ISTH
Improvements in Health-Related Quality of Life in Adults With Severe or Moderately Severe Hemophilia B After Receiving Etranacogene Dezaparvovec Gene Therapy
Presented by: Steven W. Pipe, MD, University of Michigan, Ann Arbor, Michigan, United States
R. Itzler1, J. Miller2, R. Robson2, P. Monahan3, S. Pipe4
1CSL Behring, King of Prussia, PA, USA, King of Prussia, Pennsylvania, United States
2Everest Clinical Research, Little Falls, NJ, USA, Little Falls, New Jersey, United States
3CSL Behring, King of Prussia, PA, USA, King Of Prussia, Pennsylvania, United States
4University of Michigan, Ann Arbor, Michigan, United States
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