Sorotan Dari Kongres Tahunan ke-14 EAHAD
Etranacogene Dezaparvovec (varian AAV5-Padua hFIX), Vektor yang Ditingkatkan untuk Transfer Gen pada Orang Dewasa dengan Hemofilia B Parah atau Sedang-Parah: Data Dua Tahun Dari Uji Coba Fase 2b
Annette von Drygalski, MD, PharmD1, Adam Giermasz, MD, PhD2, Giancarlo Castaman, MD3, Nigel S. Key, MBCHB4, Susan U.Lattimore, RN5, Frank WG Leebeek, MD6, Wolfgang A. Miesbach, MD, PhD7, Michael Recht, MD, PhD5, Esteban Gomez, MD8, Robert Gut, MD, PhD9, dan Steven W. Pipe, MD10
1Universitas California San Diego, La Jolla, CA, AS
2Universitas California Davis, Sacramento, CA, AS
3Azienda Ospedaliera Universitaria Careggi, Florence, Italia
4Universitas North Carolina, Chapel Hill, AS
5Universitas Kesehatan dan Sains Oregon, Portland, AS
6Pusat Medis Universitas Erasmus, Rotterdam, Belanda
7Rumah Sakit Universitas Frankfurt, Jerman
8Rumah Sakit Anak Phoenix, Phoenix, AS
9uniQure Inc, Lexington, MA, AS
10Universitas Michigan, Ann Arbor, MI, AS
Annette von Drygalski, MD, PharmD1, Adam Giermasz, MD, PhD2, Giancarlo Castaman, MD3, Nigel S. Key, MBCHB4, Susan U.Lattimore, RN5, Frank WG Leebeek, MD6, Wolfgang A. Miesbach, MD, PhD7, Michael Recht, MD, PhD5, Esteban Gomez, MD8, Robert Gut, MD, PhD9, dan Steven W. Pipe, MD10
1Universitas California San Diego, La Jolla, CA, AS
2Universitas California Davis, Sacramento, CA, AS
3Azienda Ospedaliera Universitaria Careggi, Florence, Italia
4Universitas North Carolina, Chapel Hill, AS
5Universitas Kesehatan dan Sains Oregon, Portland, AS
6Pusat Medis Universitas Erasmus, Rotterdam, Belanda
7Rumah Sakit Universitas Frankfurt, Jerman
8Rumah Sakit Anak Phoenix, Phoenix, AS
9uniQure Inc, Lexington, MA, AS
10Universitas Michigan, Ann Arbor, MI, AS