Pwen esansyèl Soti nan ISTH 2020 Kongrè a Virtual
Long-term vektè jnom Rezilta ak iminoogenicity nan AAV FVIII Transfè jèn nan emofil yon modèl la chen.
Pòl Batty1, Choong-Ryoul Sihn2, Justin Ishida2, Aomei Mo1, Bridget Yates2, Christine Brown1, Lorianne Harpell1, Abbey Pender1Chris B. Russell2, Sofia Sardo Infirri1, Richard Torres2, Andre Winterborn3Sylvia Fong2, David Lillicrap1
1Depatman Patoloji ak Medsin Molekilè, Inivèsite Rèn nan, Kingston, Ontario, Kanada.
2BioMarin famasetik, Novato, CA, USA.
3Sèvis Swen Animal, Inivèsite Rèn nan, Kingston, Ontario, Kanada.
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