Pwen esansyèl nan 14yèm Kongrè Anyèl EAHAD la
Etranacogene Dezaparvovec (AAV5-Padua hFIX variant), yon vektè amelyore pou transfè jèn nan granmoun ki gen emofil grav oswa modere-grav: de ane done ki sòti nan yon faz 2b esè.
Annette von Drygalski, MD, PharmD1, Adan Giermasz, MD, PhD2, Giancarlo Castaman, MD3, Nigel S. Key, MBchB4, Susan U. Lattimore, RN5, Frank WG Leebeek, MD6, Wolfgang A. Miesbach, MD, PhD7, Michael Recht, MD, PhD5, Esteban Gomez, MD8, Robert Gut, MD, PhD9, ak Steven W. Pipe, MD10
1Inivèsite Kalifòni San Diego, La Jolla, CA, USA
2Inivèsite Kalifòni Davis, Sacramento, CA, USA
3Azienda Ospedaliera Università Careggi, Florence, Itali
4Inivèsite North Carolina, Chapel Hill, USA
5Oregon Sante ak Syans Inivèsite, Portland, USA
6Erasmus University Medical Center, Rotterdam, Netherlands
7Lopital Inivèsite Frankfurt, Almay
8Lopital Timoun Phoenix, Phoenix, USA
9uniQure Inc, Lexington, MA, Etazini
10Inivèsite Michigan, Ann Arbor, MI, USA
Annette von Drygalski, MD, PharmD1, Adan Giermasz, MD, PhD2, Giancarlo Castaman, MD3, Nigel S. Key, MBchB4, Susan U. Lattimore, RN5, Frank WG Leebeek, MD6, Wolfgang A. Miesbach, MD, PhD7, Michael Recht, MD, PhD5, Esteban Gomez, MD8, Robert Gut, MD, PhD9, ak Steven W. Pipe, MD10
1Inivèsite Kalifòni San Diego, La Jolla, CA, USA
2Inivèsite Kalifòni Davis, Sacramento, CA, USA
3Azienda Ospedaliera Università Careggi, Florence, Itali
4Inivèsite North Carolina, Chapel Hill, USA
5Oregon Sante ak Syans Inivèsite, Portland, USA
6Erasmus University Medical Center, Rotterdam, Netherlands
7Lopital Inivèsite Frankfurt, Almay
8Lopital Timoun Phoenix, Phoenix, USA
9uniQure Inc, Lexington, MA, Etazini
10Inivèsite Michigan, Ann Arbor, MI, USA
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