Pwen esansyèl nan 15yèm Kongrè Anyèl EAHAD la
Enpak transfè jèn Valoctocogene Roxaparvovec pou emofili A grav sou kalite lavi ki gen rapò ak sante
B.O'Mahony1,2; J.Mahlangu3; K.Peerlinck4; JDWang5; G.Lowe6; CWTan7; A.Giermasz8; H.Tran9; TLKhoo10; E.Cockrell11; D.Pepperell12; H.Chambost13; MLFernández14; R.Kazmi15; E.Majerus16; MWSkinner17,18; R.Klamroth19; J.Quinn20; H.Yu20; WYWong20; A.Lawal20; TMRobinson20; B.Kim20
1Ilandè Haemophilia Society;2Trinity College, Dublin, Iland;3 Emophilia Comprehensive Care Center, Charlotte Maxeke Johannesburg Academic Hospital, University of the Witwatersrand ak NHLS, Johannesburg, Lafrik di sid;4 Depatman Medsin vaskilè ak emostaz ak sant emofili, Lopital Inivèsite Leuven, Leuven, Bèljik;5 Centerfor Maladi Ra ak Emofili, Taichung Veterans General Hospital, Taichung, Taiwan, Pwovens Lachin;6 West Midlands Comprehensive Care Haemophilia Centre, Queen Elizabeth Hospital, Birmingham, Wayòm Ini;7 Depatman ematoloji, Royal Adelaide Hospital, Adelaide, Ostrali;8 Sant Tretman Emofili, University of California Davis, Sacramento, Etazini;9 Inite emostaz ak tronboz, Sant Tretman Haemophilia, Lopital Alfred, Melbourne;10 Enstiti ematoloji, Royal Prince Alfred Hospital, Camperdown, Ostrali;11 Pedyat Hematology Oncology, Saint Joseph's Children's Hospital, Tampa, Etazini;12 Depatman Ematoloji, Lopital Fiona Stanley, Murdoch, Ostrali;13 AP-HM, Depatman Pedyat Ematoloji Onkoloji, Timoun Lopital La Timone, Aix Marseille University, INSERM, INRA, C2VN, Marseille, Frans;14 Complejo Hospitalario Universitario A Coruña, A Coruña, Espay;15 Depatman ematoloji, Southampton University Hospital, Southampton, Wayòm Ini;16 Depatman Medsin, Washington University nan St. Louis, St.17 Institute for Policy Advancement Ltd, Washington, Etazini;18 McMaster University, Hamilton, Kanada;19 Sant Tretman Emofili Swen konplè, Vivantes Klinikumim Friedrichshain, Bèlen, Almay;20 BioMarin famasetik Inc, Novato, Etazini