Pwen esansyèl nan 14yèm Kongrè Anyèl EAHAD la
Efikasite ak Sekirite nan Etranacogene Dezaparvovec nan Adilt ki gen grav oswa modere-grav Emofili B: Premye done ki soti nan faz 3 Hope-B Jij Terapi Jijman an
Steven W Pipe, MD1, Michael Recht, MD, PhD2, Nigel S Key, MBchB3, Frank WG Leebeek, MD4, Giancarlo Castaman, MD5, Susan U Lattimore, RN6, Paul van der Valk, MD6, Kathelijne Peerlinck, MD, PhD7, Michael Coppens, MD, PhD8, Niamh O'Connell, MB PhD9, K. Jan Pasi, MBChB, PhD10, Pyè Kampmann, MD11, Karina Meijer, MD, PhD.12, Annette von Drygalski, MD, PharmD13, Guy Young, MD14, Cedric Hermans, MD15, Jan Astermark, MD, PhD16, Robert Klamroth, MD, PhD17, Richard S Sitwon, MD, PhD18, Natan Visweshwar, MD19, Shelley Crary, MD20, Rashid Kazmi, MBBS21, Emily Symington, MBChB22, Miguel A Escobar, MD23, Esteban Gomez, MD24, Rebecca Kruse-Jarres, MD, MPH25, Adan Kotowski, MD26, Doris Quon, MD, PhD27, Michael Wang, MD28, Allison P Wheeler, MD29, Eileen K Sawyer, PhD30, Stephanie Verweij30, Valerie Colletta, MSc30, Naghmana Bajwa, MD, Robert Gut, MD, PD30, Wolfgang Miesbach, MD, PhD31
1Inivèsite Michigan, Ann Arbor, MI, USA
2Oregon Sante ak Syans Inivèsite, Portland, OSWA, USA
3Inivèsite North Carolina, Chapel Hill, NC, USA
4Erasmus MC, University Medical Center, Rotterdam, Netherlands
5Sant pou maladi senyen ak koagulasyon, Careggi Inivèsite Lopital, Florence, Itali
6Inivèsite Medisch Centrum Utrecht, Netherlands
7Depatman Medsin vaskilè ak Ememostazi ak Emofili Sant, Inivèsite Lopital Louvain, Louvain, Bèljik
8Depatman Medsin vaskilè, Amstèdam Syans kadyo-vaskilè, Amstèdam Inivèsite Sant Medikal, Inivèsite Amstèdam, Amstèdam, Netherlands
9Sant Koagulasyon Nasyonal la, Lopital St James a, Dublin, Iland
10Royal London Emofili Sant, Barts ak lekòl la London nan Medsin ak Dexter, London, UK
11Rigshospitalet, vil Copenhagen, Denmark
12Inivèsite Medikal Sant Groningen, Groningen, Netherlands
13Inivèsite Kalifòni San Diego, La Jolla, CA, USA
14Children's Hospital Los Angeles, University of Southern California Keck School of Medicine, Los Angeles, CA, USA
15Cliniques Universitaires Saint ‐ Luc, Université Catholique de Louvain, Brussels, Bèljik
16Lopital Inivèsite Skåne, Malmö
17Vivantes Klinikum im Friedrichshain, Bèlen, Almay
18Inivèsite Utah, Salt Lake City, UT, USA
19Inivèsite nan Sid Florid, Tampa, FL, USA
20University of Arkansas pou Syans Medikal, AR, USA
21Inivèsite Lopital Southampton NHS Fondasyon Trust; Southampton, UK
22Cambridge University - Addenbrooke's Hospital, Cambridge, UK
23Sant Syans Inivèsite Texas nan Houston, Houston, TX, USA
24Lopital Phoenix pou Timoun yo, Phoenix USA
25Bloodworks Nòdwès, Seattle, WA
26WNY BloodCare, NY, USA
27Los Angeles Orthopedic Hospital, Orthopedic Emophilia Treatment Center, Los Angeles, CA, USA
28Inivèsite Kolorado Emofili ak Sant tronbozi, Anschutz Medical Campus, Aurora, CO
29Sant Medikal Inivèsite Vanderbilt, Nashville, TN, USA
30uniQure BV, Amstèdam, Netherlands / uniQure Inc. Lexington, MA, USA
31Inivèsite lopital Frankfurt, Frankfurt, Almay
Steven W Pipe, MD1, Michael Recht, MD, PhD2, Nigel S Key, MBchB3, Frank WG Leebeek, MD4, Giancarlo Castaman, MD5, Susan U Lattimore, RN6, Paul van der Valk, MD6, Kathelijne Peerlinck, MD, PhD7, Michael Coppens, MD, PhD8, Niamh O'Connell, MB PhD9, K. Jan Pasi, MBChB, PhD10, Pyè Kampmann, MD11, Karina Meijer, MD, PhD.12, Annette von Drygalski, MD, PharmD13, Guy Young, MD14, Cedric Hermans, MD15, Jan Astermark, MD, PhD16, Robert Klamroth, MD, PhD17, Richard S Sitwon, MD, PhD18, Natan Visweshwar, MD19, Shelley Crary, MD20, Rashid Kazmi, MBBS21, Emily Symington, MBChB22, Miguel A Escobar, MD23, Esteban Gomez, MD24, Rebecca Kruse-Jarres, MD, MPH25, Adan Kotowski, MD26, Doris Quon, MD, PhD27, Michael Wang, MD28, Allison P Wheeler, MD29, Eileen K Sawyer, PhD30, Stephanie Verweij30, Valerie Colletta, MSc30, Naghmana Bajwa, MD, Robert Gut, MD, PD30, Wolfgang Miesbach, MD, PhD31
1Inivèsite Michigan, Ann Arbor, MI, USA
2Oregon Sante ak Syans Inivèsite, Portland, OSWA, USA
3Inivèsite North Carolina, Chapel Hill, NC, USA
4Erasmus MC, University Medical Center, Rotterdam, Netherlands
5Sant pou maladi senyen ak koagulasyon, Careggi Inivèsite Lopital, Florence, Itali
6Inivèsite Medisch Centrum Utrecht, Netherlands
7Depatman Medsin vaskilè ak Ememostazi ak Emofili Sant, Inivèsite Lopital Louvain, Louvain, Bèljik
8Depatman Medsin vaskilè, Amstèdam Syans kadyo-vaskilè, Amstèdam Inivèsite Sant Medikal, Inivèsite Amstèdam, Amstèdam, Netherlands
9Sant Koagulasyon Nasyonal la, Lopital St James a, Dublin, Iland
10Royal London Emofili Sant, Barts ak lekòl la London nan Medsin ak Dexter, London, UK
11Rigshospitalet, vil Copenhagen, Denmark
12Inivèsite Medikal Sant Groningen, Groningen, Netherlands
13Inivèsite Kalifòni San Diego, La Jolla, CA, USA
14Children's Hospital Los Angeles, University of Southern California Keck School of Medicine, Los Angeles, CA, USA
15Cliniques Universitaires Saint ‐ Luc, Université Catholique de Louvain, Brussels, Bèljik
16Lopital Inivèsite Skåne, Malmö
17Vivantes Klinikum im Friedrichshain, Bèlen, Almay
18Inivèsite Utah, Salt Lake City, UT, USA
19Inivèsite nan Sid Florid, Tampa, FL, USA
20University of Arkansas pou Syans Medikal, AR, USA
21Inivèsite Lopital Southampton NHS Fondasyon Trust; Southampton, UK
22Cambridge University - Addenbrooke's Hospital, Cambridge, UK
23Sant Syans Inivèsite Texas nan Houston, Houston, TX, USA
24Lopital Phoenix pou Timoun yo, Phoenix USA
25Bloodworks Nòdwès, Seattle, WA
26WNY BloodCare, NY, USA
27Los Angeles Orthopedic Hospital, Orthopedic Emophilia Treatment Center, Los Angeles, CA, USA
28Inivèsite Kolorado Emofili ak Sant tronbozi, Anschutz Medical Campus, Aurora, CO
29Sant Medikal Inivèsite Vanderbilt, Nashville, TN, USA
30uniQure BV, Amstèdam, Netherlands / uniQure Inc. Lexington, MA, USA
31Inivèsite lopital Frankfurt, Frankfurt, Almay