Pwen esansyèl ki soti nan Summit Virtual WFH 2020
Premye-nan-moun etid katwini swivi sou dirab efikasite ki ka geri ou ak sekirite: AAV jèn Terapi ak Valoctocogene Roxaparvovec pou imilit grav A
K. John Pasi, MB, ChB, PhD, FRCP, FRCPath, FRCPCH1; Savita Rangarajan, MBBS, FRCP, FRCPath2; Nina Mitchell, MB, BChir3; Èske Lester, MB, ChB, PhD, FRCP, FRCPath4; Emily Symington, BSc, MBBS, MRCP, FRCPath5; Bella Madan, MD, FRCP, FRCPath6; Michael Laffan, DM, FRCP, FRCPath7; Chris B. Russell, PhD3; Mingjin Li, MSc3; Benjamin Kim, MD, MPhil3; Glenn F. Pierce, MD, PhD8; Zèl yen wong, MD3
1Barts ak Lekòl la nan Lond Medsin ak Dexter, London, UK
2Inivèsite Lopital Southampton, Southampton, UK
3BioMarin Inc., Novato, CA, USA
4Inivèsite Lopital Birmingham NHS Foundation Trust, Birmingham, UK
5Inivèsite Cambridge Inivèsite Fondasyon NHS Trust, Cambridge, UK
6Guy's & St. Thomas 'Trust Fondasyon NHS, London, UK
7Sant pou ematoloji, Imperial Kolèj London, London, UK.
8Konsiltan, La Jolla, CA, USA
K. John Pasi, MB, ChB, PhD, FRCP, FRCPath, FRCPCH1; Savita Rangarajan, MBBS, FRCP, FRCPath2; Nina Mitchell, MB, BChir3; Èske Lester, MB, ChB, PhD, FRCP, FRCPath4; Emily Symington, BSc, MBBS, MRCP, FRCPath5; Bella Madan, MD, FRCP, FRCPath6; Michael Laffan, DM, FRCP, FRCPath7; Chris B. Russell, PhD3; Mingjin Li, MSc3; Benjamin Kim, MD, MPhil3; Glenn F. Pierce, MD, PhD8; Zèl yen wong, MD3
1Barts ak Lekòl la nan Lond Medsin ak Dexter, London, UK
2Inivèsite Lopital Southampton, Southampton, UK
3BioMarin Inc., Novato, CA, USA
4Inivèsite Lopital Birmingham NHS Foundation Trust, Birmingham, UK
5Inivèsite Cambridge Inivèsite Fondasyon NHS Trust, Cambridge, UK
6Guy's & St. Thomas 'Trust Fondasyon NHS, London, UK
7Sant pou ematoloji, Imperial Kolèj London, London, UK.
8Konsiltan, La Jolla, CA, USA