Pwen esansyèl ki soti nan reyinyon 62th ASH Anyèl ak Ekspozisyon an
Premye done ki soti nan faz 3 ESPERANS-B Jijman Terapi Jij la: efikasite ak sekirite nan Etranacogene Dezaparvovec (AAV5-Padova hFIX Variant; AMT-061) nan granmoun ki gen grav oswa modere-grav Emofili B trete irrespective of pre-egziste anti-kapsid netralizant Antikò
Steven W. Pipe, MD1, Michael Recht, MD, PhD2, Nigel S. Key, MD3, Frank WG Leebeek, MD, PhD4, Giancarlo Castaman, MD5, Susan U. Lattimore, RN6, Pòl Van Der Valk7,8,9, Kathelijne Peerlinck, MD, PhD10, Michael Coppens, MD11, Niamh O'Connell, MD, PhD12, Jan Pasi, MB, ChB, PhD, FRCP, FRCPath, FRCPCH13, Pyè Kampmann, MD14, Karina Meijer, MD, PhD15, Annette von Drygalski, MD, PharmD16, Guy Young, MD17, Cedric Hermans, MD, MRCP, PhD18, Jan Astermark, MD, PhD19,20, Robert Klamroth, MD, PhD21, Richard S. Sitwon, MD22, Natan Visweshwar, MD23, Shelley Crary, MD, MS24, Rashid Kazmi, MBBS25, Emily Symington26, Miguel A. Escobar, MD27, Esteban Gomez, MD28, Rebecca Kruse-Jarres, MD29, Adan Kotowski, MD30, Doris Quon, MD, PhD31, Michael Wang, MD32, Allison P. Wheeler, MD33, Eileen K Sawyer, PhD34, Stephanie Verweij, BSc35, Valerie Colletta, MSc36, Naghmana Bajma, MD37, Robert Gut, MD, PhD36 ak Wolfgang A. Miesbach, MD, PhD38
1University of Michigan, Ann Arbor, MI
2Oregon Sante ak Syans Inivèsite, Portland, OSWA
3Inivèsite North Carolina, Chapel Hill, NC
4Erasmus MC, University Medical Center Rotterdam, Rotterdam, Netherlands
5Azienda Ospedaliera Università Careggi, Florence, Itali
6Oregon Sante ak Syans Inivèsite, Portland
7Vrije Universiteit Medical Center, Amstèdam, NLD
8Inivèsite Medisch Centrum Utrecht, Utrecht, Netherlands
9Van Creveldkliniek, University Medical Center Utrecht, Utrecht, Netherlands
10Depatman Medsin vaskilè ak Ememostazi ak Emofili Sant, Inivèsite Lopital Louvain, Louvain, Bèljik
11Sant Medikal Amstèdam Inivèsite, Inivèsite Amstèdam, Amstèdam, Netherlands
12Sant nasyonal koagulasyon, St James Hospital, Dublin, Iland
13Royal London Emofili Sant, Barts ak lekòl la London nan Medsin ak Dexter, London, Wayòm Ini
14Rigshospitalet, vil Copenhagen, Denmark
15Inivèsite Medikal Sant Groningen, Groningen, Netherlands
16Inivèsite Kalifòni San Diego, La Jolla, CA
17University of Southern California Keck School of Medicine, Children's Hospital Los Angeles, Los Angeles, CA
18Cliniques Universitaires Saint-Luc, Universite Catholique de Louvain, Brussels, Bèljik
19Depatman Translational Medsin-klinik koagulasyon, Lund University, Malmo, Syèd
20Lopital Inivèsite Skane, Malmo, Syèd
21Vivantes Klinikum im Friedrichshain, Bèlen, Almay
22Inivèsite Utah, Salt Lake City, UT
23University of South Florida, Tampa, FL
24University of Arkansas pou Syans Medikal, Little Rock, AR
25Inivèsite Lopital Southampton NHS Fondasyon Trust, Southampton, Wayòm Ini
26Lopital Cambridge University – Addenbrooke a, Cambridge, Wayòm Ini
27Sant Syans Inivèsite Texas nan Houston, Houston, TX
28Lopital Timoun Phoenix, Phoenix, AZ
29Bloodworks Nòdwès, Seattle, WA
30Emofili Sant nan lwès New York, New York
31Los Angeles Orthopedic Hospital, Orthopedic Emophilia Treatment Center, Los Angeles, CA
32Anschutz Medical Campus, University of Colorado, Lekòl Medsin, Emofili ak Sant tronbozi, Aurora, CO
33Sant Medikal Inivèsite Vanderbilt, Nashville, TN
34uniQure Inc, Lexington, MA
35uniQure, Lexington, MA
36uniQure Inc, Lexington, MA
37Uniqure Inc, Lexington, MA
38Inivèsite lopital Frankfurt, Frankfurt, Almay
Steven W. Pipe, MD1, Michael Recht, MD, PhD2, Nigel S. Key, MD3, Frank WG Leebeek, MD, PhD4, Giancarlo Castaman, MD5, Susan U. Lattimore, RN6, Pòl Van Der Valk7,8,9, Kathelijne Peerlinck, MD, PhD10, Michael Coppens, MD11, Niamh O'Connell, MD, PhD12, Jan Pasi, MB, ChB, PhD, FRCP, FRCPath, FRCPCH13, Pyè Kampmann, MD14, Karina Meijer, MD, PhD15, Annette von Drygalski, MD, PharmD16, Guy Young, MD17, Cedric Hermans, MD, MRCP, PhD18, Jan Astermark, MD, PhD19,20, Robert Klamroth, MD, PhD21, Richard S. Sitwon, MD22, Natan Visweshwar, MD23, Shelley Crary, MD, MS24, Rashid Kazmi, MBBS25, Emily Symington26, Miguel A. Escobar, MD27, Esteban Gomez, MD28, Rebecca Kruse-Jarres, MD29, Adan Kotowski, MD30, Doris Quon, MD, PhD31, Michael Wang, MD32, Allison P. Wheeler, MD33, Eileen K Sawyer, PhD34, Stephanie Verweij, BSc35, Valerie Colletta, MSc36, Naghmana Bajma, MD37, Robert Gut, MD, PhD36 ak Wolfgang A. Miesbach, MD, PhD38
1University of Michigan, Ann Arbor, MI
2Oregon Sante ak Syans Inivèsite, Portland, OSWA
3Inivèsite North Carolina, Chapel Hill, NC
4Erasmus MC, University Medical Center Rotterdam, Rotterdam, Netherlands
5Azienda Ospedaliera Università Careggi, Florence, Itali
6Oregon Sante ak Syans Inivèsite, Portland
7Vrije Universiteit Medical Center, Amstèdam, NLD
8Inivèsite Medisch Centrum Utrecht, Utrecht, Netherlands
9Van Creveldkliniek, University Medical Center Utrecht, Utrecht, Netherlands
10Depatman Medsin vaskilè ak Ememostazi ak Emofili Sant, Inivèsite Lopital Louvain, Louvain, Bèljik
11Sant Medikal Amstèdam Inivèsite, Inivèsite Amstèdam, Amstèdam, Netherlands
12Sant nasyonal koagulasyon, St James Hospital, Dublin, Iland
13Royal London Emofili Sant, Barts ak lekòl la London nan Medsin ak Dexter, London, Wayòm Ini
14Rigshospitalet, vil Copenhagen, Denmark
15Inivèsite Medikal Sant Groningen, Groningen, Netherlands
16Inivèsite Kalifòni San Diego, La Jolla, CA
17University of Southern California Keck School of Medicine, Children's Hospital Los Angeles, Los Angeles, CA
18Cliniques Universitaires Saint-Luc, Universite Catholique de Louvain, Brussels, Bèljik
19Depatman Translational Medsin-klinik koagulasyon, Lund University, Malmo, Syèd
20Lopital Inivèsite Skane, Malmo, Syèd
21Vivantes Klinikum im Friedrichshain, Bèlen, Almay
22Inivèsite Utah, Salt Lake City, UT
23University of South Florida, Tampa, FL
24University of Arkansas pou Syans Medikal, Little Rock, AR
25Inivèsite Lopital Southampton NHS Fondasyon Trust, Southampton, Wayòm Ini
26Lopital Cambridge University – Addenbrooke a, Cambridge, Wayòm Ini
27Sant Syans Inivèsite Texas nan Houston, Houston, TX
28Lopital Timoun Phoenix, Phoenix, AZ
29Bloodworks Nòdwès, Seattle, WA
30Emofili Sant nan lwès New York, New York
31Los Angeles Orthopedic Hospital, Orthopedic Emophilia Treatment Center, Los Angeles, CA
32Anschutz Medical Campus, University of Colorado, Lekòl Medsin, Emofili ak Sant tronbozi, Aurora, CO
33Sant Medikal Inivèsite Vanderbilt, Nashville, TN
34uniQure Inc, Lexington, MA
35uniQure, Lexington, MA
36uniQure Inc, Lexington, MA
37Uniqure Inc, Lexington, MA
38Inivèsite lopital Frankfurt, Frankfurt, Almay