Pwen esansyèl ki soti nan reyinyon 62th ASH Anyèl ak Ekspozisyon an
AMT-060 Terapi jèn nan adilt ki gen emofili grav oswa modere-grav B konfime ki eksprime ekspresyon fiks ak rediksyon dirab nan senyen ak faktè IX konsomasyon pou jiska 5 an
Frank WG Leebeek, MD, PhD1, Karina Meijer, MD, PhD2, Michael Coppens, MD3, Pyè Kampmann, MD4, Robert Klamroth, MD, PhD5, Roger Schutgens, MD, PhD, MSc6, Giancarlo Castaman, MD7, Erhard Seifried, MD, PhD8, Joachim Schwaeble9, Halvard Bönig1,10, Eileen KK Sawyer, PhD11, ak Wolfgang A. Miesbach, MD12
1Sant Medikal Inivèsite Erasmus, Rotterdam, Netherlands
2Depatman ematoloji, University of Groningen, University Medical Center Groningen, Groningen, Netherlands
3Sant Medikal Amstèdam Inivèsite, Inivèsite Amstèdam, Amstèdam, Netherlands
4Rigshospitalet, vil Copenhagen, Denmark
5Depatman Medsin Entèn, Medsin vaskilè ak ememostazoloji, Vivantes Klinikum im Friedrichshain, Bèlen, Almay
6Van Creveldkliniek, Inivèsite Sant Medikal Utrecht, Utrecht University, Utrecht, Netherlands
7Azienda Ospedaliera Università Careggi, Florence, Itali
8Enstiti Frankfurt, Alman Sèvis Kwa Wouj san Baden Wurtemberg-Hessen, Frankfurt, Almay
9Enstiti Frankfurt, Alman Sèvis Kwa Wouj san Baden-Wurtemberg-Hessen, Frankfurt, Almay
10Inivèsite Washington Lekòl Medsin, Seattle, WA
11uniQure Inc., Lexington, MA
12Universitatsklinikum Frankfurt, Frankfurt, Almay
Frank WG Leebeek, MD, PhD1, Karina Meijer, MD, PhD2, Michael Coppens, MD3, Pyè Kampmann, MD4, Robert Klamroth, MD, PhD5, Roger Schutgens, MD, PhD, MSc6, Giancarlo Castaman, MD7, Erhard Seifried, MD, PhD8, Joachim Schwaeble9, Halvard Bönig1,10, Eileen KK Sawyer, PhD11, ak Wolfgang A. Miesbach, MD12
1Sant Medikal Inivèsite Erasmus, Rotterdam, Netherlands
2Depatman ematoloji, University of Groningen, University Medical Center Groningen, Groningen, Netherlands
3Sant Medikal Amstèdam Inivèsite, Inivèsite Amstèdam, Amstèdam, Netherlands
4Rigshospitalet, vil Copenhagen, Denmark
5Depatman Medsin Entèn, Medsin vaskilè ak ememostazoloji, Vivantes Klinikum im Friedrichshain, Bèlen, Almay
6Van Creveldkliniek, Inivèsite Sant Medikal Utrecht, Utrecht University, Utrecht, Netherlands
7Azienda Ospedaliera Università Careggi, Florence, Itali
8Enstiti Frankfurt, Alman Sèvis Kwa Wouj san Baden Wurtemberg-Hessen, Frankfurt, Almay
9Enstiti Frankfurt, Alman Sèvis Kwa Wouj san Baden-Wurtemberg-Hessen, Frankfurt, Almay
10Inivèsite Washington Lekòl Medsin, Seattle, WA
11uniQure Inc., Lexington, MA
12Universitatsklinikum Frankfurt, Frankfurt, Almay