Pwen esansyèl nan 15yèm Kongrè Anyèl EAHAD la
Analiz final ki soti nan Faz Pivotal 3 Esè Terapi Jenetik HOPE-B: Efikasite Eta Stab ak Sekirite Etranacogene Dezaparvovec nan Adilt ak Emofili B grav oswa modere grav.
Wolfgang Miesbach1; Frank WGLeebeek2; Michael Recht3; Nigel S. Key4; Susan Lattimore3; Giancarlo Castaman5; Michael Coppens6; David Cooper7; Sergio Slawka7; Stephanie Verweij7; Robert Gut7; Ricardo Dolmetsch7; Yanyan Li8; Pòl E. Monahan8; Steven W. Pipe9
Envestigatè HOPE-B1; Inivèsite lopital Frankfurt, Frankfurt, Almay2; Erasmus MC, University Medical Center Rotterdam, Netherlands3; Oregon Health & Science University, Portland, OR, Etazini4; University of North Carolina, Chapel Hill, NC, Etazini5; Sant pou maladi senyen ak koagulasyon, Careggi University Hospital, Florence, Itali6; Amstèdam University Medical Centers, University of Amstèdam, Amstèdam, Netherlands7; uniQureBV, Amstèdam, Netherlands/uniQure Inc. Lexington, MA, USA8; CSL Behring, Wa Lapris, PA, Etazini9; University of Michigan, Ann Arbor, MI, Etazini