Pwen esansyèl nan 14yèm Kongrè Anyèl EAHAD la
AMT-060 Terapi jèn nan adilt ki gen emofili grav oswa modere-grav B konfime ki eksprime ekspresyon fiks ak rediksyon dirab nan senyen ak faktè IX konsomasyon pou jiska 5 an
Frank WG Leebeek, MD, PhD1, Karina Meijer, MD, PhD2, Michael Coppens, MD, PhD3, Pyè Kampmann, MD4, Robert Klamroth, MD5, Roger Schutgens, MD, PhD, MSc6, Giancarlo Castaman, MD7, Erhard Seifried, MD, PhD8, Joachim Schwaeble, MD9, Halvard Bönig, MD1,10, Eileen K. Sawyer, PhD11, ak Wolfgang Miesbach, MD, PhD12
1Sant Medikal Inivèsite Erasmus, Rotterdam, Netherlands
2Inivèsite Medikal Sant Groningen, Groningen, Netherlands
3Sant Medikal Amstèdam Inivèsite, Amstèdam, Netherlands
4Rigshospitalet, vil Copenhagen, Denmark
5Vivantes Klinikum, Bèlen, Almay
6Van Creveldkliniek, Inivèsite Sant Medikal Utrecht, Utrecht University, Utrecht, Netherlands
7Azienda Ospedaliera Università Careggi, Florence, Itali
8Enstiti Frankfurt, Alman Sèvis Kwa Wouj san Baden Wurtemberg-Hessen, Frankfurt, Almay
9Enstiti Frankfurt, Alman Sèvis Kwa Wouj san Baden Wurtemberg-Hessen, Frankfurt, Almay
10Inivèsite Washington, Seattle, WA
11uniQure Inc., Lexington, MA
12Inivèsite lopital Frankfurt, Frankfurt, Almay
Frank WG Leebeek, MD, PhD1, Karina Meijer, MD, PhD2, Michael Coppens, MD, PhD3, Pyè Kampmann, MD4, Robert Klamroth, MD5, Roger Schutgens, MD, PhD, MSc6, Giancarlo Castaman, MD7, Erhard Seifried, MD, PhD8, Joachim Schwaeble, MD9, Halvard Bönig, MD1,10, Eileen K. Sawyer, PhD11, ak Wolfgang Miesbach, MD, PhD12
1Sant Medikal Inivèsite Erasmus, Rotterdam, Netherlands
2Inivèsite Medikal Sant Groningen, Groningen, Netherlands
3Sant Medikal Amstèdam Inivèsite, Amstèdam, Netherlands
4Rigshospitalet, vil Copenhagen, Denmark
5Vivantes Klinikum, Bèlen, Almay
6Van Creveldkliniek, Inivèsite Sant Medikal Utrecht, Utrecht University, Utrecht, Netherlands
7Azienda Ospedaliera Università Careggi, Florence, Itali
8Enstiti Frankfurt, Alman Sèvis Kwa Wouj san Baden Wurtemberg-Hessen, Frankfurt, Almay
9Enstiti Frankfurt, Alman Sèvis Kwa Wouj san Baden Wurtemberg-Hessen, Frankfurt, Almay
10Inivèsite Washington, Seattle, WA
11uniQure Inc., Lexington, MA
12Inivèsite lopital Frankfurt, Frankfurt, Almay