Buaicphointí Ón 14ú Comhdháil Bhliantúil de EAHAD
Etranacogene Dezaparvovec (leagan AAV5-Padua hFIX), Veicteoir Feabhsaithe le haghaidh Aistriú Géinte in Aosaigh le Hemophilia B Trom nó Measartha-Dian: Sonraí Dhá Bhliana ó Thriail Chéim 2b
Annette von Drygalski, MD, PharmD1, Adam Giermasz, MD, PhD2, Giancarlo Castaman, MD3, Nigel S. Eochair, MBChB4, Susan U. Lattimore, RN5, Frank WG Leebeek, MD6, Wolfgang A. Miesbach, MD, PhD7, Michael Recht, MD, PhD5, Esteban Gomez, MD8, Robert Gut, MD, PhD9, agus Steven W. Pipe, MD10
1Ollscoil California San Diego, La Jolla, CA, SAM
2Ollscoil California Davis, Sacramento, CA, SAM
3Azienda Ospedaliera Universitaria Careggi, Florence, an Iodáil
4Ollscoil Carolina Thuaidh, Chapel Hill, SAM
5Ollscoil Sláinte agus Eolaíochta Oregon, Portland, SAM
6Ionad Leighis Ollscoil Erasmus, Rotterdam, An Ísiltír
7Ospidéal na hOllscoile Frankfurt, an Ghearmáin
8Ospidéal Leanaí an Fhionnuisce, an Fhionnuisce, SAM
9uniQure Inc, Lexington, MA, SAM
10Ollscoil Michigan, Ann Arbor, MI, SAM
Annette von Drygalski, MD, PharmD1, Adam Giermasz, MD, PhD2, Giancarlo Castaman, MD3, Nigel S. Eochair, MBChB4, Susan U. Lattimore, RN5, Frank WG Leebeek, MD6, Wolfgang A. Miesbach, MD, PhD7, Michael Recht, MD, PhD5, Esteban Gomez, MD8, Robert Gut, MD, PhD9, agus Steven W. Pipe, MD10
1Ollscoil California San Diego, La Jolla, CA, SAM
2Ollscoil California Davis, Sacramento, CA, SAM
3Azienda Ospedaliera Universitaria Careggi, Florence, an Iodáil
4Ollscoil Carolina Thuaidh, Chapel Hill, SAM
5Ollscoil Sláinte agus Eolaíochta Oregon, Portland, SAM
6Ionad Leighis Ollscoil Erasmus, Rotterdam, An Ísiltír
7Ospidéal na hOllscoile Frankfurt, an Ghearmáin
8Ospidéal Leanaí an Fhionnuisce, an Fhionnuisce, SAM
9uniQure Inc, Lexington, MA, SAM
10Ollscoil Michigan, Ann Arbor, MI, SAM