Buaicphointí ó Chruinniú Mullaigh Fíorúil WFH 2020
Staidéar Leantach Ceithre bliana den chéad duine ar Éifeachtúlacht agus Sábháilteacht Teiripeach Inmharthana: Teiripe Géine AAV le Roxaparvovec Valoctocogene do Haemophilia Trom A
K. John Pasi, MB, CHB, PhD, FRCP, FRCPath, FRCPCH1; Savita Rangarajan, MBBS, FRCP, FRCPath2; Nina Mitchell, MB, BChir3; Will Lester, MB, CHB, PhD, FRCP, FRCPath4; Emily Symington, BSc, MBBS, MRCP, FRCPath5; Bella Madan, MD, FRCP, FRCPath6; Michael Laffan, DM, FRCP, FRCPath7; Chris B. Russell, PhD3; Mingjin Li, MSc3; Benjamin Kim, MD, MPhil3; Glenn F. Pierce, MD, PhD8; Sciathán Yen Wong, MD3
1Barts agus Scoil an Leighis agus na Fiaclóireachta i Londain, Londain, an Ríocht Aontaithe
2Ospidéal na hOllscoile Southampton, Southampton, an Ríocht Aontaithe
3BioMarin Pharmaceutical Inc., Novato, CA, SAM
4Iontaobhas Fondúireachta NHS Ospidéil na hOllscoile, Birmingham, an Ríocht Aontaithe
5Iontaobhas Fondúireachta NHS Ospidéil Ollscoil Cambridge, Cambridge, an Ríocht Aontaithe
6Iontaobhas Fondúireachta NHS Guy's & St. Thomas, Londain, an Ríocht Aontaithe
7Ionad Haemaiteolaíochta, Imperial College London, London, UK.
8Comhairleoir, La Jolla, CA, SAM
K. John Pasi, MB, CHB, PhD, FRCP, FRCPath, FRCPCH1; Savita Rangarajan, MBBS, FRCP, FRCPath2; Nina Mitchell, MB, BChir3; Will Lester, MB, CHB, PhD, FRCP, FRCPath4; Emily Symington, BSc, MBBS, MRCP, FRCPath5; Bella Madan, MD, FRCP, FRCPath6; Michael Laffan, DM, FRCP, FRCPath7; Chris B. Russell, PhD3; Mingjin Li, MSc3; Benjamin Kim, MD, MPhil3; Glenn F. Pierce, MD, PhD8; Sciathán Yen Wong, MD3
1Barts agus Scoil an Leighis agus na Fiaclóireachta i Londain, Londain, an Ríocht Aontaithe
2Ospidéal na hOllscoile Southampton, Southampton, an Ríocht Aontaithe
3BioMarin Pharmaceutical Inc., Novato, CA, SAM
4Iontaobhas Fondúireachta NHS Ospidéil na hOllscoile, Birmingham, an Ríocht Aontaithe
5Iontaobhas Fondúireachta NHS Ospidéil Ollscoil Cambridge, Cambridge, an Ríocht Aontaithe
6Iontaobhas Fondúireachta NHS Guy's & St. Thomas, Londain, an Ríocht Aontaithe
7Ionad Haemaiteolaíochta, Imperial College London, London, UK.
8Comhairleoir, La Jolla, CA, SAM