Buaicphointí ó Chruinniú Mullaigh Fíorúil WFH 2020
Dul chun cinn le déanaí i bhforbairt AMT-061 (Etranacogene Dezaparvovec) do Dhaoine a bhfuil Hemophilia B Trom nó Measartha Trom orthu
Steven W. Píob,1 Wolfgang Miesbach,2 Annette Von Drygalski,3 Adam Giermasz,4 Karina Meijer,5 Michael Coppens,6 Peadar Kampmann,7 Robert Klamroth,8 Roger Schutgens,9 Nigel S. Eochair,10 Susan Lattimore,11 Michael Recht,12 Esteban Gomez,13 Giancarlo Castaman,14 Eileen K. Sawyer,12 Robert Gut,12 Frank WG Leebeek15
1Ollscoil Michigan, Ann Arbor, SAM
2Ospidéal na hOllscoile Frankfurt, Frankfurt, an Ghearmáin
3Ollscoil California San Diego, San Diego, SAM
4Ollscoil California Davis, Sacramento, SAM
5Ionad Leighis na hOllscoile Groningen, Groningen, an Ísiltír
6Ionad Leighis Acadúil, Amstardam, An Ísiltír
7Rigshospitalet, Cóbanhávan, an Danmhairg
8Vivantes Klinikum, Beirlín, an Ghearmáin
9Ionad Leighis na hOllscoile, Utrecht, An Ísiltír
10Ollscoil Carolina Thuaidh, Chapel Hill, SAM
11Ollscoil Sláinte & Eolaíochta Oregon, Portland, SAM
12biopharma uniQure BV, Lexington, MA, SAM
13Ospidéal Leanaí an Fhionnuisce, Phoenix USA
14Azienda Ospedaliera Universitaria Careggi, Florence, an Iodáil
15Ionad Leighis Ollscoil Erasmus, Rotterdam, An Ísiltír
Steven W. Píob,1 Wolfgang Miesbach,2 Annette Von Drygalski,3 Adam Giermasz,4 Karina Meijer,5 Michael Coppens,6 Peadar Kampmann,7 Robert Klamroth,8 Roger Schutgens,9 Nigel S. Eochair,10 Susan Lattimore,11 Michael Recht,12 Esteban Gomez,13 Giancarlo Castaman,14 Eileen K. Sawyer,12 Robert Gut,12 Frank WG Leebeek15
1Ollscoil Michigan, Ann Arbor, SAM
2Ospidéal na hOllscoile Frankfurt, Frankfurt, an Ghearmáin
3Ollscoil California San Diego, San Diego, SAM
4Ollscoil California Davis, Sacramento, SAM
5Ionad Leighis na hOllscoile Groningen, Groningen, an Ísiltír
6Ionad Leighis Acadúil, Amstardam, An Ísiltír
7Rigshospitalet, Cóbanhávan, an Danmhairg
8Vivantes Klinikum, Beirlín, an Ghearmáin
9Ionad Leighis na hOllscoile, Utrecht, An Ísiltír
10Ollscoil Carolina Thuaidh, Chapel Hill, SAM
11Ollscoil Sláinte & Eolaíochta Oregon, Portland, SAM
12biopharma uniQure BV, Lexington, MA, SAM
13Ospidéal Leanaí an Fhionnuisce, Phoenix USA
14Azienda Ospedaliera Universitaria Careggi, Florence, an Iodáil
15Ionad Leighis Ollscoil Erasmus, Rotterdam, An Ísiltír