Highlights From the ISTH 2020 Virtual Congress
Frequency, Location and Nature of AAV Vector Insertions After Long-term Follow-up of FVIII Transgene Delivery in a Hemophilia A Dog Model
Paul Batty1, Sylvia Fong2, Matteo Franco3, Irene Gil-Farina3, Aomei Mo1, Lorianne Harpell1, Christine Hough1, David Hurlbut1, Abbey Pender1, Sofia Sardo Infirri1, Andrew Winterborn4, Manfred Schmidt3 and David Lillicrap1
1Department of Pathology and Molecular Medicine, Queen's University, Kingston, Ontario, Canada.
2BioMarin Pharmaceutical, Novato, CA, USA.
3GeneWerk GmbH, Heidelberg, Germany.
3Animal Care Services, Queen's University, Kingston, Ontario, Canada.
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