First Approval of Gene Therapy in Hemophilia
Watch the Latest Conference Briefs to Learn More
Updates on Three Ongoing Clinical Trials on Adults with Severe Hemophilia B
Steven W. Pipe, MD...
Rapid Clearance of Vector Following AAV-Mediated FVIII Gene Transfer in the Phase I/II Trial of SPK-8011 in People With Hemophilia A
Benjamin J. Samelson Jones, MD, PhD...
Relationship Between Transgene-Produced FVIII and Bleeding Rates 2 Years After Gene Transfer With Valoctocogene Roxaparvovec: Results From Gener8-1
Johnny Mahlangu, BSc, MBBCh, MMed, FCPath...
Elucidating the Mechanism Behind the AAV-Derived Factor VIII Assay Discrepancy
Anna Sternberg, PhD...
Stabilin-2 Promoter Modulates the Immune Response to FVIII After Lentiviral Vector Delivery in Hemophilic Mice
Antonia Follenzi, MD, PhD...
Impact of Valoctocogene Roxaparvovec Gene Transfer for Severe Haemophilia A on Health-related Quality of Life
Johnny Mahlangu, BSc, MBBCh, MMed, FCPath...