Aipagarrienak EAHADen XIV
Adeno-Associated Virus (AAV) Gene Terapia (FLT180a) berriaren jarraipena FIX Jarduera-maila arruntak lortzen B Hemofilia B (HB) gaixoetan
(B-AMAZE Azterketa)
Pratima Chowdary,1,2 Susan Shapiro,3 Mike Makris,4 Gillian Evans,5 Sara Boyce,6 Kate hizketan,7 Gerry Dolan,8 Ulrike Reiss,9 Mark Phillips,1,2 Anne Riddell,1 Maria Rita Peralta,1 Michelle Quaye,2 Ted Tuddenham,1 Andrew Smith,10 Alison Long,10 Julie Krop,10 Amit Nathwani1,2
1Katharine Dormandy Haemophilia and Thrombosis Center, Royal Free Hospital, Londres, Erresuma Batua
2London College University, Londres, Erresuma Batua
3Oxford Haemophilia Center, Oxford, Erresuma Batua
4Sheffieldeko Unibertsitatea, Sheffield, Erresuma Batua
5Kent eta Canterbury Ospitalea, Canterbury, Erresuma Batua
6Southampton Unibertsitateko Ospitalea, Southampton, Erresuma Batua
7Newcastle Haemophilia Comprehensive Care Center, Newcastle, Erresuma Batua
8St Thomas 'eta Guy's Hospital, Londres, Erresuma Batua
9St Jude Children's Research, Memphis, TN, AEB
10Freeline, Stevenage, Erresuma Batua
Pratima Chowdary,1,2 Susan Shapiro,3 Mike Makris,4 Gillian Evans,5 Sara Boyce,6 Kate hizketan,7 Gerry Dolan,8 Ulrike Reiss,9 Mark Phillips,1,2 Anne Riddell,1 Maria Rita Peralta,1 Michelle Quaye,2 Ted Tuddenham,1 Andrew Smith,10 Alison Long,10 Julie Krop,10 Amit Nathwani1,2
1Katharine Dormandy Haemophilia and Thrombosis Center, Royal Free Hospital, Londres, Erresuma Batua
2London College University, Londres, Erresuma Batua
3Oxford Haemophilia Center, Oxford, Erresuma Batua
4Sheffieldeko Unibertsitatea, Sheffield, Erresuma Batua
5Kent eta Canterbury Ospitalea, Canterbury, Erresuma Batua
6Southampton Unibertsitateko Ospitalea, Southampton, Erresuma Batua
7Newcastle Haemophilia Comprehensive Care Center, Newcastle, Erresuma Batua
8St Thomas 'eta Guy's Hospital, Londres, Erresuma Batua
9St Jude Children's Research, Memphis, TN, AEB
10Freeline, Stevenage, Erresuma Batua