Podcasts

What Do Hemophilia Treatment Centers Need to Consider Now in Preparation for the Anticipated Availability of Gene Therapy?

What Do Hemophilia Treatment Centers Need to Consider Now in Preparation for the Anticipated Availability of Gene Therapy?

Presented by Steven W. Pipe, MD and Nigel Key, MB, ChB. FRCP

Interpreting Vector Doses in Hemophilia Gene Therapy Clinical Trials

Interpreting Vector Doses in Hemophilia Gene Therapy Clinical Trials

Presented by Steven W. Pipe, MD and Nigel Key, MB, ChB. FRCP

Hemophilia Gene Therapy in Patients With History of Inhibitors

Hemophilia Gene Therapy in Patients With History of Inhibitors

Presented by Steven W. Pipe, MD and Nigel Key, MB, ChB. FRCP

Laboratory Measurement of Hemophilia Gene Therapy Products/Factor Activity

Laboratory Measurement of Hemophilia Gene Therapy Products/Factor Activity

Presented by Steven W. Pipe, MD and Nigel Key, MB, ChB. FRCP

Adeno-Associated Virus (AAV) Mediated Gene Transfer: Why is This the Predominant Strategy for Hemophilia Gene Therapy?

Adeno-Associated Virus (AAV) Mediated Gene Transfer: Why is This the Predominant Strategy for Hemophilia Gene Therapy?

Presented by Steven W. Pipe, MD and Nigel Key, MB, ChB. FRCP

Part 1: Pre-existing Immunity Against AAV Serotypes and What This Means for Hemophilia Gene Therapy Clinical Trials

Part 1: Pre-existing Immunity Against AAV Serotypes and What This Means for Hemophilia Gene Therapy Clinical Trials

Presented by Steven W. Pipe, MD and Nigel Key, MB, ChB. FRCP

Part 2: Pre-existing Immunity Against AAV Serotypes and What This Means for Hemophilia Gene Therapy Clinical Trials

Part 2: Pre-existing Immunity Against AAV Serotypes and What This Means for Hemophilia Gene Therapy Clinical Trials

Presented by Steven W. Pipe, MD and Nigel Key, MB, ChB. FRCP

Long-Term Monitoring Following Hemophilia Gene Therapy

Long-Term Monitoring Following Hemophilia Gene Therapy

Presented by Steven W. Pipe, MD and Nigel Key, MB, ChB. FRCP

Highlights from the NHF 15th Workshop on Novel Technologies and Gene Transfer for Hemophilia

Highlights from the NHF 15th Workshop on Novel Technologies and Gene Transfer for Hemophilia

Presented by David Lillicrap, MD and Glenn F. Peirce, MD, PhD