Hemophilia Treatment Center - Case Studies

Gene therapy for hemophilia B has just received approval from both the EMA and FDA. A 20-year-old patient with severe hemophilia B comes to your HTC for a regular visit and expresses interest in getting treatment with gene therapy. How would you respond to the following questions regarding the decision making process, the administration of treatment, and post-treatment monitoring?

Watch Wolfgang Miesbach, MD and his Colleagues Discuss Treatment Questions

Download Treatment Question Responses from Steve Pipe, MD and his Colleagues

watch gene therapy experts discuss questions regarding the decision making process, the administration of treatment, and post-treatment monitoring
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Supported through educational grants from BioMarin, CSL Behring, Pfizer Inc., Roche, and Spark Therapeutics

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