Conference Coverage from Orlando

Conference Coverage from Orlando, featuring expert interviews on the latest advances in Gene Therapy.

EARN CME CREDIT

Conference Coverage – Live from Orlando 2019

Recent Updates on Gene Therapy Clinical Trials in Hemophilia B

Long term Safety and Efficacy Data from Gene Therapy Trials in Hemophilia Provide Optimism

Long term Expression of AAV mediated FVIII Gene Transfer and Vector Integration Events in Hemophilia

Novel Approaches to Hemophilia Gene Therapy in Preclinical Development

Preexisting Antibodies to AAV and Consequences for Hemophilia Gene Therapy

The Future of Hemophilia Gene Therapy

Preparing for the Approval of Gene Therapy for Hemophilia

Highlights from the NHF 15th Workshop on Novel Technologies and Gene Transfer for Hemophilia

Presented by: David Lillicrap, MD and Glenn F. Pierce, MD, PhD
September 13-14, 2019 • Washington, DC

Conference Coverage from ISTH 2019 in Melbourne

Conference Coverage from ISTH 2019 in Melbourne, featuring expert interviews on the latest advances in Gene Therapy.

EARN CME CREDIT

Conference Coverage – ISTH 2019 in Melbourne

The ALTA Study: SB-525 Gene Therapy in Adults with Hemophilia A

Prevalence of Preexisting AAV Antibodies and Implications for Gene Therapy in Hemophilia

Results of the AMT-060 and AMT-061 Gene Therapy Trials in Patients with Hemophilia B

Initial Results of the Phase 1/2 Alta Study: SB-525 Gene Therapy in Adults with Hemophilia A

One Year Follow-up of Patients with Hemophilia B Following SPK-9001 Gene Transfer

AMT-061 Gene Transfer in Adults with Hemophilia B: Early Results of a Phase 2b Trial

Current Status of Gene Therapy for Hemophilia

FLT180a: Next Generation AAV Vector for Hemophilia B

Stable Expression of FIX: Updated Results of the AMT-060 Gene Therapy Trial in Patients with Hemophilia B.

Lentiviral Vector-based Factor VIII and Factor IX Gene Therapy in Non-human Primates

Valoctocogene Roxaparvovec AAV Gene Therapy for Patients with Hemophilia A: New Results

Looking Ahead at Gene Therapy for Hemophilia

Person on the Street - ISTH 2019 in Melbourne

Watch as attendees from the ISTH 2019 Congress in Melbourne, Australia, discuss their reactions to the session on Gene Therapy in Hemophilia.

Product Theater- ISTH 2019 Melbourne

Watch as Flora Peyvandi, MD, PhD and K. John Pasi, MB ChB, PhD, FRCP, FRCPath, FRCPCH announce the launch of Gene Therapy in Hemophilia: An ISTH Education Initiative

Baseline Survey Poster

Poster

Poster Presented at the ISTH 2019 Congress
Sunday, July 7 • 18:30 – 19:30
Abstract/Poster #: PB1724
Melbourne, Australia

In early 2019, ISTH organized a group of world-renowned experts from the global hemophilia community to develop a survey to identify unmet educational needs specific to gene therapy in hemophilia. The survey was distributed online to an international audience. The results demonstrated that many need more education on the fundamentals of gene therapy and a better understanding of gene therapy as a treatment approach for hemophilia A and B.

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Educational Roadmap

ISTH's Educational Roadmap–Guiding Education for the Future
Preparing You to Answer These Critical Questions

Coming December 2019

LIVE from Orlando, 61st ASH Annual Meeting & Exposition

Featuring congress highlights and expert interviews.

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Supported by educational grants from BioMarin, Pfizer, Inc., Shire, Spark Therapeutics, and uniQure, Inc.

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Conference Coverage from Orlando

Conference Coverage – Live from Orlando 2019

Highlights from the NHF 15th Workshop on Novel Technologies and Gene Transfer for Hemophilia

Conference Coverage from ISTH 2019 in Melbourne

Conference Coverage – ISTH 2019 in Melbourne

Person on the Street - ISTH 2019 in Melbourne

Product Theater- ISTH 2019 Melbourne

Baseline Survey Poster

Educational Roadmap

ISTH's Educational Roadmap–Guiding Education for the Future
Preparing You to Answer These Critical Questions

Coming December 2019

LIVE from Orlando, 61st ASH Annual Meeting & Exposition

About

Supported by educational grants from BioMarin, Pfizer, Inc., Shire, Spark Therapeutics, and uniQure, Inc.

What Are You Looking For?

Popular Tags

Conference Coverage from Orlando

Conference Coverage – Live from Orlando 2019

Highlights from the NHF 15th Workshop on Novel Technologies and Gene Transfer for Hemophilia

Conference Coverage from ISTH 2019 in Melbourne

Conference Coverage – ISTH 2019 in Melbourne

Person on the Street - ISTH 2019 in Melbourne

Product Theater- ISTH 2019 Melbourne

Baseline Survey Poster

Educational Roadmap

ISTH's Educational Roadmap–Guiding Education for the Future Preparing You to Answer These Critical Questions

Coming December 2019

LIVE from Orlando, 61st ASH Annual Meeting & Exposition

About

Supported by educational grants from BioMarin, Pfizer, Inc., Shire, Spark Therapeutics, and uniQure, Inc.

ISTH's Educational Roadmap–Guiding Education for the Future
Preparing You to Answer These Critical Questions