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Home
About
Roadmap
Steering Committee
About ISTH
Blog
Topics
Basics of Hemophilia
Fundamental of Gene Therapies
Practical Considerations of Gene Therapies
Clinical Trial Efficacy and Safety
Patient Journey: Implementation to Lived Experience
Clinical Perspectives/Real-World Evidence
Roles of the Multidisciplinary Team
Recent Updates and Ongoing Efforts
Education
Resources Builder
Shared Decision Making
HTC Case Studies
EXPLORE Modules
Illustrated Clinical Trials
Interactive Webinars
Podcasts
Roadmap
Gene Therapy Resources
Conference Coverage
Microlearning
Monthly Roundup
News
Learning Tiers
Introductory
Intermediate
Advanced
Home
About
Roadmap
Steering Committee
About ISTH
Blog
Topics
Basics of Hemophilia
Fundamental of Gene Therapies
Practical Considerations of Gene Therapies
Clinical Trial Efficacy and Safety
Patient Journey: Implementation to Lived Experience
Clinical Perspectives/Real-World Evidence
Roles of the Multidisciplinary Team
Recent Updates and Ongoing Efforts
Education
Resources Builder
Shared Decision Making
HTC Case Studies
EXPLORE Modules
Illustrated Clinical Trials
Interactive Webinars
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Roadmap
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Conference Coverage
HIV Comorbid Infection and Liver-directed AAV-Based Gene Therapy in Adults With Severe and Moderately Severe Hemophilia B
19 December 2023
Long-term Bleeding Protection, Sustained FIX Activity, Reduction of FIX Consumption, and Safety of Hemophilia B Gene Therapy
19 December 2023
Development of adeno-associated virus (AAV5) variants capable of reducing the immunogenicity by targeting antigenic residues on the capsid surface
18 December 2023
Updates on SPK-8011
31 July 2023
Phase 3 HOPE-B Trial of etranacogene dezaparvovec in Severe/Moderately Severe Hemophilia B
31 July 2023
Updates from the GENEr8-1 Trial
31 July 2023
Residual Burden of Liver Disease After HCV-clearance in Hemophilia: A Word of Caution in the Era of Gene Therapy
31 July 2023
Efficacy and Safety of Fidanacogene Elaparvovec in Adults With Moderately Severe or Severe Hemophilia B: Results From the Phase 3 BENEGENE-2 Gene Therapy Trial
31 July 2023
Elucidating the Mechanism Behind the AAV-Derived Factor VIII Assay Discrepancy
11 July 2022
Relationship Between Transgene-Produced FVIII and Bleeding Rates 2 Years After Gene Transfer With Valoctocogene Roxaparvovec: Results From Gener8-1
11 July 2022
Results from B-LIEVE, a Phase 1/2 Dose-Confirmation Study of FLT180a AAV Gene Therapy in Patients With Hemophilia B
11 July 2022
Stable Hemostatic Correction and Improved Hemophilia-Related Quality of Life: Final Analysis from the Pivotal Phase 3 HOPE-B Trial of Etranacogene Dezaparvovec
27 June 2022
Stabilin-2 Promoter Modulates the Immune Response to FVIII After Lentiviral Vector Delivery in Hemophilic Mice
21 June 2022
Delivery of CRISPR/Cas9 mRNA LNPs to Repair a Small Deletion in FVIII Gene in Hemophilia A Mice
21 June 2022
A Factor VIII Variant With Elimination of the N-glycosylation Site at 2118 Reduced Anti-FVIII Immune Responses in Gene Therapy Treated Hemophilia A Mice
21 June 2022
Using the World Federation of Haemophilia Gene Therapy Registry for the Long-term Follow-up of Haemophilia Patients Treated with Gene Therapy
07 June 2022
Subcategories
Highlights From the 17th Annual Congress of EAHAD
Highlights From the 65th ASH Annual Meeting and Exposition
Highlights From the ESGCT 30th Annual Congress
Highlights From the 31st Congress of ISTH
Highlights From the 32nd Congress of ISTH
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Home
About
Roadmap
Steering Committee
About ISTH
Blog
Topics
Basics of Hemophilia
Fundamental of Gene Therapies
Practical Considerations of Gene Therapies
Clinical Trial Efficacy and Safety
Patient Journey: Implementation to Lived Experience
Clinical Perspectives/Real-World Evidence
Roles of the Multidisciplinary Team
Recent Updates and Ongoing Efforts
Education
Resources Builder
Shared Decision Making
HTC Case Studies
EXPLORE Modules
Illustrated Clinical Trials
Interactive Webinars
Podcasts
Roadmap
Gene Therapy Resources
Conference Coverage
Microlearning
Monthly Roundup
News
Learning Tiers
Introductory
Intermediate
Advanced
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