Highlights From the ASGCT 25th Annual Meeting
Delivery of CRISPR/Cas9 mRNA LNPs to Repair a Small Deletion in FVIII Gene in Hemophilia A Mice
Presented by: Chun-Yu Chen, PhD, Fellow-PhD | Immunity & Immunotherapies, Seattle Children's Seattle, Washington, United States
Chun-Yu Chen1, Cai Xiaohe1, Carol Miao1,2
1Seattle Children’s Research Institute, Seattle, Washington
2Department of Pediatrics, University of Washington, Seattle, Washington
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