Højdepunkter fra den 15. årlige kongres for EAHAD
Indvirkning af Valoctocogene Roxaparvovec-genoverførsel for svær hæmofili A på sundhedsrelateret livskvalitet
B.O'Mahony1,2; J. Mahlangu3; K.Peerlinck4; JDWang5; G. Lowe6; CWTan7; A. Giermasz8; H.Tran9; TLKhoo10; E. Cockrell11; D. Pepperell12; H.Chambost13; MFLFernández14; R.Kazmi15; E.Majerus16; MWSkinner17,18; R.Klamroth19; J. Quinn20; H.Yu20; WYWong20; A.Lawal20; TMRobinson20; B.Kim20
1Irish Haemophilia Society;2Trinity College, Dublin, Irland;3 Hemophilia Comprehensive Care Center, Charlotte Maxeke Johannesburg Academic Hospital, University of the Witwatersrand og NHLS, Johannesburg, Sydafrika;4 Institut for Vaskulær Medicin og Hæmostase og Hæmofili Center, Universitetshospitalerne Leuven, Leuven, Belgien;5 Center for sjældne sygdomme og hæmofili, Taichung Veterans General Hospital, Taichung, Taiwan, provinsen Kina;6 West Midlands Comprehensive Care Haemophilia Centre, Queen Elizabeth Hospital, Birmingham, Storbritannien;7 Hæmatologisk afdeling, Royal Adelaide Hospital, Adelaide, Australien;8 Hemophilia Treatment Center, University of California Davis, Sacramento, USA;9 Hæmostase og tromboseenhed, Haemophilia Treatment Centre, The Alfred Hospital, Melbourne;10 Institute of Haematology, Royal Prince Alfred Hospital, Camperdown, Australien;11 Pædiatrisk hæmatologisk onkologi, Saint Joseph's Children's Hospital, Tampa, USA;12 Hæmatologisk afdeling, Fiona Stanley Hospital, Murdoch, Australien;13 AP-HM, afdelingen for pædiatrisk hæmatologisk onkologi, børnehospitalet La Timone, Aix Marseille Universitet, INSERM, INRA, C2VN, Marseille, Frankrig;14 Complejo Hospitalario Universitario A Coruña, A Coruña, Spanien;15 Department of Haematology, Southampton University Hospital, Southampton, Storbritannien;16 Institut for Medicin, Washington University i St. Louis, St. Louis;17 Institute for Policy Advancement Ltd, Washington, USA;18 McMaster University, Hamilton, Canada;19 Comprehensive Care Haemophilia Treatment Center, Vivantes Klinikumim Friedrichshain, Berlin, Tyskland;20 BioMarin Pharmaceutical Inc., Novato, USA