Højdepunkter fra den 14. årlige kongres for EAHAD
Etranacogene Dezaparvovec (AAV5-Padua hFIX-variant), en forbedret vektor til genoverførsel hos voksne med svær eller moderat-svær hæmofili B: To års data fra et fase 2b forsøg
Annette von Drygalski, MD, PharmD1, Adam Giermasz, MD, ph.d.2, Giancarlo Castaman, MD3, Nigel S. Key, MBChB4, Susan U. Lattimore, RN5, Frank WG Leebeek, MD6, Wolfgang A. Miesbach, MD, ph.d.7, Michael Recht, MD, ph.d.5, Esteban Gomez, MD8, Robert Gut, MD, ph.d.9og Steven W. Pipe, MD10
1University of California San Diego, La Jolla, CA, USA
2University of California Davis, Sacramento, CA, USA
3Azienda Ospedaliera Universitaria Careggi, Firenze, Italien
4University of North Carolina, Chapel Hill, USA
5Oregon Health and Science University, Portland, USA
6Erasmus University Medical Center, Rotterdam, Holland
7Universitetshospital Frankfurt, Tyskland
8Phoenix børnehospital, Phoenix, USA
9uniQure Inc, Lexington, MA, USA
10University of Michigan, Ann Arbor, MI, USA
Annette von Drygalski, MD, PharmD1, Adam Giermasz, MD, ph.d.2, Giancarlo Castaman, MD3, Nigel S. Key, MBChB4, Susan U. Lattimore, RN5, Frank WG Leebeek, MD6, Wolfgang A. Miesbach, MD, ph.d.7, Michael Recht, MD, ph.d.5, Esteban Gomez, MD8, Robert Gut, MD, ph.d.9og Steven W. Pipe, MD10
1University of California San Diego, La Jolla, CA, USA
2University of California Davis, Sacramento, CA, USA
3Azienda Ospedaliera Universitaria Careggi, Firenze, Italien
4University of North Carolina, Chapel Hill, USA
5Oregon Health and Science University, Portland, USA
6Erasmus University Medical Center, Rotterdam, Holland
7Universitetshospital Frankfurt, Tyskland
8Phoenix børnehospital, Phoenix, USA
9uniQure Inc, Lexington, MA, USA
10University of Michigan, Ann Arbor, MI, USA