Højdepunkter fra WFH Virtual Summit 2020
Seneste fremskridt i udviklingen af AMT-061 (Etranacogene Dezaparvovec) for personer med alvorlig eller moderat alvorlig hæmofili B
Steven W. Pipe,1 Wolfgang Miesbach,2 Annette Von Drygalski,3 Adam Giermasz,4 Karina Meijer,5 Michiel Coppens,6 Peter Kampmann,7 Robert Klamroth,8 Roger Schutgens,9 Nigel S.Nøgle,10 Susan Lattimore,11 Michael Recht,12 Esteban Gomez,13 Giancarlo Castaman,14 Eileen K. Sawyer,12 Robert Gut,12 Frank WG Leebeek15
1University of Michigan, Ann Arbor, USA
2Universitetshospital Frankfurt, Frankfurt am Main, Tyskland
3University of California San Diego, San Diego, USA
4University of California Davis, Sacramento, USA
5University Medical Center Groningen, Groningen, Holland
6Academic Medical Center, Amsterdam, Holland
7Rigshospitalet, København, Danmark
8Vivantes Klinikum, Berlin, Tyskland
9University Medical Center, Utrecht, Holland
10University of North Carolina, Chapel Hill, USA
11Oregon Health & Science University, Portland, USA
12uniQure biopharma BV, Lexington, MA, USA
13Phoenix børnehospital, Phoenix USA
14Azienda Ospedaliera Universitaria Careggi, Firenze, Italien
15Erasmus University Medical Center, Rotterdam, Holland
Steven W. Pipe,1 Wolfgang Miesbach,2 Annette Von Drygalski,3 Adam Giermasz,4 Karina Meijer,5 Michiel Coppens,6 Peter Kampmann,7 Robert Klamroth,8 Roger Schutgens,9 Nigel S.Nøgle,10 Susan Lattimore,11 Michael Recht,12 Esteban Gomez,13 Giancarlo Castaman,14 Eileen K. Sawyer,12 Robert Gut,12 Frank WG Leebeek15
1University of Michigan, Ann Arbor, USA
2Universitetshospital Frankfurt, Frankfurt am Main, Tyskland
3University of California San Diego, San Diego, USA
4University of California Davis, Sacramento, USA
5University Medical Center Groningen, Groningen, Holland
6Academic Medical Center, Amsterdam, Holland
7Rigshospitalet, København, Danmark
8Vivantes Klinikum, Berlin, Tyskland
9University Medical Center, Utrecht, Holland
10University of North Carolina, Chapel Hill, USA
11Oregon Health & Science University, Portland, USA
12uniQure biopharma BV, Lexington, MA, USA
13Phoenix børnehospital, Phoenix USA
14Azienda Ospedaliera Universitaria Careggi, Firenze, Italien
15Erasmus University Medical Center, Rotterdam, Holland